Assessment of a symptomatic Duchenne muscular dystrophy carrier 20years after myoblast transplantation from her asymptomatic identical twin sister

Neuromuscular Disorders

Volumn 23, Issue 7, 2013, Pages 575-579

  Hogrel, Jean Yves ^a   Zagnoli, Fabien ^b   Canal, Aurélie ^a   Fraysse, Bodvael ^a   Bouchard, Jean Pierre ^c   Skuk, Daniel ^c   Fardeau, Michel ^a   Tremblay, Jacques P ^c  

^a PITIÉ SALPÊTRIÈRE HOSPITAL   (France)

^b Military Teaching Hospital Clermont Tonnerre   (France)

^c UNIVERSITÉ LAVAL   (Canada)

Author keywords

Cell therapy; Duchenne muscular dystrophy; Monozygotic twin; Outcome measures; Unequal lyonisation

Indexed keywords

DYSTROPHIN;

ADULT; ANAMNESIS; ARTICLE; ASSISTED VENTILATION; CASE REPORT; CELL TRANSPLANTATION; CLINICAL EFFECTIVENESS; CONTROLLED STUDY; DUCHENNE MUSCULAR DYSTROPHY; FALLING; FEMALE; HEART EJECTION FRACTION; HUMAN; HUMAN TISSUE; MOTOR PERFORMANCE; MUSCLE STRENGTH; MYOBLAST; POWERED WHEELCHAIR; PRIORITY JOURNAL; RESPIRATORY FAILURE; TRACHEOTOMY; TREATMENT RESPONSE; TWINS; VITAL CAPACITY;

CELL- AND TISSUE-BASED THERAPY; FEMALE; HUMANS; MUSCULAR DYSTROPHY, DUCHENNE; MUTATION; MYOBLASTS; TREATMENT OUTCOME; TWINS, MONOZYGOTIC;

EID: 84878986847     PISSN: 09608966     EISSN: 18732364     Source Type: Journal    
DOI: 10.1016/j.nmd.2013.04.007     Document Type: Article

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