Developing outcome measures for pediatric mitochondrial disorders: Which complaints and limitations are most burdensome to patients and their parents?

Mitochondrion

Volumn 13, Issue 1, 2013, Pages 15-24

  Koene, Saskia ^a   Wortmann, Saskia B ^a   de Vries, Maaike C ^a   Jonckheere, An I ^a   Morava, Eva ^a   de Groot, Imelda J M ^a   Smeitink, Jan A M ^a  

^a RADBOUD UNIVERSITY MEDICAL CENTER   (Netherlands)

Author keywords

Clinical trial; Mitochondrial disease; Outcome measures; Patient perspective

Indexed keywords

ADOLESCENT; ARTICLE; BEHAVIOR; CHILD; DAILY LIFE ACTIVITY; DISORDERS OF MITOCHONDRIAL FUNCTIONS; EPILEPSY; FATIGUE; FEMALE; HUMAN; MAJOR CLINICAL STUDY; MALE; MUSCLE WEAKNESS; OUTCOME ASSESSMENT; PARENT; PEDIATRICS; PRESCHOOL CHILD; PRIORITY JOURNAL; QUESTIONNAIRE; SCHOOL CHILD; SPEECH DISORDER; SYMPTOM;

ADOLESCENT; CHILD; CHILD, PRESCHOOL; COST OF ILLNESS; FEMALE; HUMANS; INFANT; MALE; MITOCHONDRIAL DISEASES; PARENTS; QUESTIONNAIRES; TREATMENT OUTCOME;

EID: 84873316509     PISSN: 15677249     EISSN: 18728278     Source Type: Journal    
DOI: 10.1016/j.mito.2012.11.002     Document Type: Article

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