Eltrombopag for the treatment of the inherited thrombocytopenia deriving from MYH9 mutations
Pecci A, Gresele P, Klersy C et al. Eltrombopag for the treatment of the inherited thrombocytopenia deriving from MYH9 mutations. Blood 2010; 116: 5832-5870.
Short-term eltrombopag for surgical preparation of a patient with inherited thrombocytopenia deriving from MYH9 mutation
Pecci A, Barozzi S, d'Amico S et al. Short-term eltrombopag for surgical preparation of a patient with inherited thrombocytopenia deriving from MYH9 mutation. Thromb Haemost 2012; 107:1188-1189.
Eltrombopag can stimulate trilineage hematopoiesis with transfusion independence in patients with refractory severe aplastic anemia: Results from a phase II trial
Olnes MJ, Scheinberg P, Calvo K et al. Eltrombopag can stimulate trilineage hematopoiesis with transfusion independence in patients with refractory severe aplastic anemia: results from a phase II trial. Blood (Annual Meeting Abstracts), 2011; 118: 54.
Phase I clinical study of eltrombopag, an oral, nonpeptide thrombopoietin receptor agonist
Jenkins JM, Williams D, Deng Y et al. Phase I clinical study of eltrombopag, an oral, nonpeptide thrombopoietin receptor agonist. Blood 2007; 109: 4739-4741.
TERC and TERT gene mutations in patients with bone marrow failure and the significance of telomere length measurements
Du HY, Pumbo E, Ivanovich J et al. TERC and TERT gene mutations in patients with bone marrow failure and the significance of telomere length measurements. Blood 2009; 113: 309.
Recent advances in the understanding and management of MYH9-re-lated inherited thrombocytopenias
Balduini CL, Pecci A, Savoia A. Recent advances in the understanding and management of MYH9-re-lated inherited thrombocytopenias. Br J Hematol 2011; 154: 161-174.
Megakaryocytes of patients with MYH9-related thrombocytopenia present an altered proplatelet formation
Pecci A, Malara A, Badalucco S et al. Megakaryocytes of patients with MYH9-related thrombocytopenia present an altered proplatelet formation. Thromb Haemost 2009; 102: 90-96.