Cell and gene therapy for genetic diseases: Inherited disorders affecting the lung and those mimicking sudden infant death syndrome

Human Gene Therapy

Volumn 23, Issue 6, 2012, Pages 548-556

  Keeler, Allison M ^a   Flotte, Terence R ^a  

^a UNIVERSITY OF MASSACHUSETTS MEDICAL SCHOOL   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ACYL COENZYME A DEHYDROGENASE; ACYL COENZYME A DEHYDROGENASE 9; ADENOVIRUS VECTOR; E1A PROTEIN; E1B PROTEIN; E3 PROTEIN; LONG CHAIN ACYL COENZYME A DEHYDROGENASE; MEDIUM CHAIN ACYL COENZYME A DEHYDROGENASE; MUTANT PROTEIN; PANCREAS ENZYME; PIZ PROTEIN; SERINE PROTEINASE INHIBITOR; TRANSMEMBRANE CONDUCTANCE REGULATOR; UNCLASSIFIED DRUG; VERY LONG CHAIN ACYL COENZYME A DEHYDROGENASE; VIRUS PROTEIN;

ALPHA 1 ANTITRYPSIN DEFICIENCY; ARTICLE; CELL THERAPY; CHROMOSOME 17; CYSTIC FIBROSIS; DISORDERS OF LIPID METABOLISM; ELECTRON TRANSPORT; EMBRYONIC STEM CELL; FATTY ACID OXIDATION; FATTY ACID OXIDATION DISORDER; GENE THERAPY; GENETIC DISORDER; HEMATOPOIETIC STEM CELL; HUMAN; LIPOSOMAL GENE DELIVERY SYSTEM; LUNG DISEASE; NONHUMAN; NONVIRAL GENE THERAPY; NUTRITIONAL SUPPORT; SUDDEN INFANT DEATH SYNDROME; VIRAL GENE THERAPY;

GENETIC THERAPY; HUMANS; INFANT; LUNG DISEASES; SUDDEN INFANT DEATH; TISSUE THERAPY;

ADENO-ASSOCIATED VIRUS; ADENOVIRIDAE;

EID: 84864346895     PISSN: 10430342     EISSN: 15577422     Source Type: Journal    
DOI: 10.1089/hum.2012.087     Document Type: Article

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