Source document verification in the Mucopolysaccharidosis Type I Registry

Pharmacoepidemiology and Drug Safety

Volumn 21, Issue 7, 2012, Pages 749-752

  Verhulst, Karien ^a   Artiles Carloni, Laura ^b   Beck, Michael ^c   Clarke, Joe T R ^d   Neto, Jordao Correa ^e   Cox, Gerald F ^b,f   Fernhoff, Paul M ^g   Guffon, Nathalie ^h   Kong, Yuan ^b   Martins, Ana Maria ⁱ   Tylki Szymanska, Anna ^j   Whitley, Chester B ^k   Wijburg, Frits A ^l   Wraith, Edward J ^m   Koepper, Catherine M ^b  

^a Genzyme Europe BV   (Netherlands)

^b GENZYME CORPORATION   (United States)

^c JOHANNES GUTENBERG UNIVERSITY   (Germany)

^d HOSPITAL FOR SICK CHILDREN   (Canada)

^e Department of Genetics   (Brazil)

^f BOSTON CHILDREN S HOSPITAL   (United States)

^g EMORY UNIVERSITY SCHOOL OF MEDICINE   (United States)

^h HOSPICES CIVILS DE LYON   (France)

ⁱ FEDERAL UNIVERSITY OF SÃO PAULO   (Brazil)

^j CHILDREN'S MEMORIAL HEALTH INSTITUTE   (Poland)

^k UNIVERSITY OF MINNESOTA MEDICAL CENTER   (United States)

^l UNIVERSITY OF AMSTERDAM   (Netherlands)

^m UNIVERSITY OF MANCHESTER   (United Kingdom)

more..

Author keywords

Enzyme replacement therapy; Laronidase; MPS I; Registry; Source document verification

Indexed keywords

LARONIDASE;

ACCURACY; ARTICLE; DATA ANALYSIS; DATA BASE; DISEASE REGISTRY; EUROPE; FOLLOW UP; HUMAN; HURLER SYNDROME; INFORMATION PROCESSING; MEDICAL DOCUMENTATION; NORTH AMERICA; PRIORITY JOURNAL; SOUTH AND CENTRAL AMERICA; SYSTEMATIC ERROR;

EID: 84863545549     PISSN: 10538569     EISSN: 10991557     Source Type: Journal    
DOI: 10.1002/pds.2200     Document Type: Article

References (6)

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