The quick motor function test: A new tool to rate clinical severity and motor function in Pompe patients

Journal of Inherited Metabolic Disease

Volumn 35, Issue 2, 2012, Pages 317-323

  Van Capelle, Carine I ^a   Van Der Beek, Nadine A M E ^a   De Vries, Juna M ^a   Van Doorn, Pieter A ^a   Duivenvoorden, Hugo J ^a   Leshner, Robert T ^b   Hagemans, Marloes L C ^a   Van Der Ploeg, Ans T ^a  

^a ERASMUS MEDICAL CENTER   (Netherlands)

^b GEORGE WASHINGTON UNIVERSITY   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

RECOMBINANT GLUCAN 1,4 ALPHA GLUCOSIDASE;

ADULT; AGED; ARTICLE; CHILD; CLINICAL ASSESSMENT; CONTROLLED STUDY; DIAGNOSTIC TEST ACCURACY STUDY; DISEASE SEVERITY; DYNAMOMETER; FEMALE; FUNCTIONAL ASSESSMENT; GLYCOGEN STORAGE DISEASE TYPE 2; GROSS MOTOR FUNCTION MEASURE; HUMAN; INTERRATER RELIABILITY; IPA ERASMUS MC POMPE SURVEY; MAJOR CLINICAL STUDY; MALE; MANUAL MUSCLE TEST; MOTOR PERFORMANCE; MUSCLE EXAMINATION; MUSCLE FUNCTION; MUSCLE STRENGTH; MUSCLE WEAKNESS; MUSCULOSKELETAL SYSTEM EXAMINATION; PRESCHOOL CHILD; PSYCHOMETRY; QUICK MOTOR FUNCTION TEST; RECEIVER OPERATING CHARACTERISTIC; TREATMENT OUTCOME;

ADOLESCENT; ADULT; AGED; CHILD; CHILD, PRESCHOOL; COHORT STUDIES; DISABILITY EVALUATION; FEMALE; GLYCOGEN STORAGE DISEASE TYPE II; HUMANS; MALE; MIDDLE AGED; MUSCLE STRENGTH; OUTCOME ASSESSMENT (HEALTH CARE); PSYCHOMETRICS; REPRODUCIBILITY OF RESULTS; SURVIVAL RATE; YOUNG ADULT;

EID: 84863451773     PISSN: 01418955     EISSN: 15732665     Source Type: Journal    
DOI: 10.1007/s10545-011-9388-3     Document Type: Article

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