Gene therapy for haemophilia B

Haemophilia

Volumn 18, Issue SUPPL.4, 2012, Pages 13-17

  Tuddenham, E ^a  

^a ROYAL FREE LONDON NHS FOUNDATION TRUST   (United Kingdom)

Author keywords

AAV; Clinical trial; Gene therapy; Haemophilia B

Indexed keywords

ALANINE AMINOTRANSFERASE; BLOOD CLOTTING FACTOR 9; PARVOVIRUS VECTOR; PREDNISOLONE; RECOMBINANT BLOOD CLOTTING FACTOR 9;

ALANINE AMINOTRANSFERASE BLOOD LEVEL; ARTICLE; CLINICAL TRIAL (TOPIC); DISEASE SEVERITY; DRUG EFFICACY; DRUG INFUSION; DRUG SAFETY; HEMOPHILIA B; HUMAN; HYPERTRANSAMINASEMIA; NONHUMAN; PRIORITY JOURNAL; SHORT COURSE THERAPY; SIDE EFFECT; TREATMENT OUTCOME; VIRAL GENE THERAPY;

ADENOVIRIDAE; DEPENDOVIRUS; FACTOR IX; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HEMOPHILIA B; HUMANS;

EID: 84862882940     PISSN: 13518216     EISSN: 13652516     Source Type: Journal    
DOI: 10.1111/j.1365-2516.2012.02823.x     Document Type: Article

References (9)

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