New motor outcome function measures in evaluation of Late-Onset Pompe disease before and after enzyme replacement therapy

Muscle and Nerve

Volumn 45, Issue 6, 2012, Pages 831-834

  Angelini, Corrado ^a,b   Semplicini, Claudio ^a   Ravaglia, Sabrina ^c,d   Moggio, Maurizio ^e   Comi, Giacomo P ^e   Musumeci, Olimpia ^f   Pegoraro, Elena ^a   Tonin, Paola ^g   Filosto, Massimiliano ^h   Servidei, Serenella ⁱ   Morandi, Lucia ^j   Crescimanno, Grazia ^k   Marrosu, Giovanni ^l   Siciliano, Gabriele ^m   Mongini, Tiziana ⁿ   Toscano, Antonio ^f   Sette, E ^o   Tugnoli, V ^o   Parini, R ^o   Rigoldi, M ^o   Donati, M D ^o   Gasperini, S ^o   Vercelli, L ^o   Barca, E ^o   Di Giacopo, R ^o   Pasanisi, M B ^o   Bembi, B ^o   Lucchini, V ^o   Piras, R ^o   Ricci, G ^o   Di Iorio, G ^o   Diodato, D ^o   Carubbi, F ^o   Ariatti, A ^o   more..

^a UNIVERSITY OF PADOVA   (Italy)

^b IRCCS SAN CAMILLO HOSPITAL   (Italy)

^c UNIVERSITY OF PAVIA   (Italy)

^d Clinical Institute Beato Matteo   (Italy)

^e UNIVERSITY OF MILAN   (Italy)

^f UNIVERSITY OF MESSINA   (Italy)

^g UNIVERSITY OF VERONA   (Italy)

^h SPEDALI CIVILI   (Italy)

ⁱ CATHOLIC UNIVERSITY   (Italy)

^j DEPARTMENT OF NEUROSURGERY   (Italy)

^k VILLA SOFIA CERVELLO HOSPITAL   (Italy)

^l UNIVERSITY OF CAGLIARI   (Italy)

^m UNIVERSITY OF PISA   (Italy)

ⁿ UNIVERSITY OF TURIN   (Italy)

^o NONE

more..

Author keywords

Enzyme replacement therapy; Glycogen storage type II; Outcome measures; Protocol; Trial

Indexed keywords

ALPHA GLUCOSIDASE;

ADULT; AGED; ARTICLE; CLINICAL ARTICLE; CORRELATION ANALYSIS; ENZYME REPLACEMENT; FEMALE; GAIT; GLYCOGEN STORAGE DISEASE TYPE 2; HUMAN; MALE; MOTOR PERFORMANCE; OUTCOME ASSESSMENT; PRIORITY JOURNAL; SCORING SYSTEM; WALKING;

ADULT; AGE OF ONSET; AGED; DISABILITY EVALUATION; ENZYME REPLACEMENT THERAPY; FEMALE; FOLLOW-UP STUDIES; GAIT; GLYCOGEN STORAGE DISEASE TYPE II; HUMANS; MALE; MIDDLE AGED; MOTOR ACTIVITY; OUTCOME ASSESSMENT (HEALTH CARE); TREATMENT OUTCOME; WALKING;

EID: 84860912447     PISSN: 0148639X     EISSN: 10974598     Source Type: Journal    
DOI: 10.1002/mus.23340     Document Type: Article

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