메뉴 건너뛰기




Volumn 45, Issue 6, 2012, Pages 796-802

Early corticosteroid treatment in 4 duchenne muscular dystrophy patients: 14-year follow-up

Author keywords

Alternate day regimen; Corticosteroid therapy; Duchenne muscular dystrophy; Outcome; Prospective study

Indexed keywords

DEFLAZACORT; PREDNISONE;

EID: 84860896654     PISSN: 0148639X     EISSN: 10974598     Source Type: Journal    
DOI: 10.1002/mus.23272     Document Type: Article
Times cited : (97)

References (46)
  • 1
    • 19944427852 scopus 로고    scopus 로고
    • Practice parameter: corticosteroid treatment of Duchenne dystrophy: report of the Quality Standards Subcommittee of the American Academy of Neurology and the Practice Committee of the Child Neurology Society
    • Moxley RT III, Ashwal S, Pandya S, Connolly A, Florence J, Mathews K, et al. Practice parameter: corticosteroid treatment of Duchenne dystrophy: report of the Quality Standards Subcommittee of the American Academy of Neurology and the Practice Committee of the Child Neurology Society. Neurology 2005; 64: 13-20.
    • (2005) Neurology , vol.64 , pp. 13-20
    • Moxley III, R.T.1    Ashwal, S.2    Pandya, S.3    Connolly, A.4    Florence, J.5    Mathews, K.6
  • 2
    • 72149108443 scopus 로고    scopus 로고
    • Diagnosis and management of Duchenne muscular dystrophy, 1: diagnosis, and pharmacological and psychosocial management
    • Bushby K, Finkel R, Birnkrant DJ, Case LE, Clemens PR, Cripe L, et al. Diagnosis and management of Duchenne muscular dystrophy, 1: diagnosis, and pharmacological and psychosocial management. Lancet Neurol 2010; 9: 77-93.
    • (2010) Lancet Neurol , vol.9 , pp. 77-93
    • Bushby, K.1    Finkel, R.2    Birnkrant, D.J.3    Case, L.E.4    Clemens, P.R.5    Cripe, L.6
  • 3
    • 0642275758 scopus 로고    scopus 로고
    • Deflazacort for the treatment of Duchenne Dystrophy: a systematic review
    • Campbell C, Jacob P. Deflazacort for the treatment of Duchenne Dystrophy: a systematic review. BMC Neurol 2003; 3: 7.
    • (2003) BMC Neurol , vol.3 , pp. 7
    • Campbell, C.1    Jacob, P.2
  • 5
    • 77956322846 scopus 로고    scopus 로고
    • Change in natural history of Duchenne muscular dystrophy with long-term corticosteroid treatment: implications for management
    • Moxley RTIII, Pandya S, Ciafaloni E, Fox DJ, Campbell K. Change in natural history of Duchenne muscular dystrophy with long-term corticosteroid treatment: implications for management. J Child Neurol 2010; 25: 1116-1129.
    • (2010) J Child Neurol , vol.25 , pp. 1116-1129
    • Moxley III, R.T.1    Pandya, S.2    Ciafaloni, E.3    Fox, D.J.4    Campbell, K.5
  • 6
    • 27544464241 scopus 로고    scopus 로고
    • Corticosteroid treatment and functional improvement in Duchenne muscular dystrophy: long-term effect
    • Balaban B, Matthews DJ, Clayton GH, Carry T. Corticosteroid treatment and functional improvement in Duchenne muscular dystrophy: long-term effect. Am J Phys Med Rehabil 2005; 84: 843-850.
    • (2005) Am J Phys Med Rehabil , vol.84 , pp. 843-850
    • Balaban, B.1    Matthews, D.J.2    Clayton, G.H.3    Carry, T.4
  • 7
    • 33646478253 scopus 로고    scopus 로고
    • Long-term benefits of deflazacort treatment for boys with Duchenne muscular dystrophy in their second decade
    • Biggar WD, Harris VA, Eliasoph L, Alman B. Long-term benefits of deflazacort treatment for boys with Duchenne muscular dystrophy in their second decade. Neuromuscul Disord 2006; 16: 249-255.
    • (2006) Neuromuscul Disord , vol.16 , pp. 249-255
    • Biggar, W.D.1    Harris, V.A.2    Eliasoph, L.3    Alman, B.4
  • 8
    • 43449112637 scopus 로고    scopus 로고
    • Corticosteroid treatment retards development of ventricular dysfunction in Duchenne muscular dystrophy
    • Markham LW, Kinnett K, Wong BL, Woodrow Benson D, Cripe LH. Corticosteroid treatment retards development of ventricular dysfunction in Duchenne muscular dystrophy. Neuromuscul Disord 2008; 18: 365-370.
    • (2008) Neuromuscul Disord , vol.18 , pp. 365-370
    • Markham, L.W.1    Kinnett, K.2    Wong, B.L.3    Woodrow Benson, D.4    Cripe, L.H.5
  • 9
    • 33947182922 scopus 로고    scopus 로고
    • Effect of long-term steroids on cough efficiency and respiratory muscle strength in patients with Duchenne muscular dystrophy
    • Daftary AS, Crisanti M, Kalra M, Wong B, Amin R. Effect of long-term steroids on cough efficiency and respiratory muscle strength in patients with Duchenne muscular dystrophy. Pediatrics 2007; 119: e320-e324.
    • (2007) Pediatrics , vol.119
    • Daftary, A.S.1    Crisanti, M.2    Kalra, M.3    Wong, B.4    Amin, R.5
  • 10
    • 34248201124 scopus 로고    scopus 로고
    • Orthopedic outcomes of long-term daily corticosteroid treatment in Duchenne muscular dystrophy
    • King WM, Ruttencutter R, Nagaraja HN, Matkovic V, Landoll J, Hoyle C, et al. Orthopedic outcomes of long-term daily corticosteroid treatment in Duchenne muscular dystrophy. Neurology 2007; 68: 1607-1613.
    • (2007) Neurology , vol.68 , pp. 1607-1613
    • King, W.M.1    Ruttencutter, R.2    Nagaraja, H.N.3    Matkovic, V.4    Landoll, J.5    Hoyle, C.6
  • 13
    • 0036166717 scopus 로고    scopus 로고
    • Vertebral compression in Duchenne muscular dystrophy following deflazacort
    • Talim B, Malaguti C, Gnudi S, Politano L, Merlini L. Vertebral compression in Duchenne muscular dystrophy following deflazacort. Neuromuscul Disord 2002; 12: 294-295.
    • (2002) Neuromuscul Disord , vol.12 , pp. 294-295
    • Talim, B.1    Malaguti, C.2    Gnudi, S.3    Politano, L.4    Merlini, L.5
  • 14
    • 0036042524 scopus 로고    scopus 로고
    • Remission of clinical signs in early Duchenne muscular dystrophy on intermittent low-dosage prednisolone therapy
    • Dubowitz V, Kinali M, Main M, Mercuri E, Muntoni F. Remission of clinical signs in early Duchenne muscular dystrophy on intermittent low-dosage prednisolone therapy. Eur J Paediatr Neurol 2002; 6: 153-159.
    • (2002) Eur J Paediatr Neurol , vol.6 , pp. 153-159
    • Dubowitz, V.1    Kinali, M.2    Main, M.3    Mercuri, E.4    Muntoni, F.5
  • 15
    • 0036823601 scopus 로고    scopus 로고
    • An effective, low-dosage, intermittent schedule of prednisolone in the long-term treatment of early cases of Duchenne dystrophy
    • Kinali M, Mercuri E, Main M, Muntoni F, Dubowitz V. An effective, low-dosage, intermittent schedule of prednisolone in the long-term treatment of early cases of Duchenne dystrophy. Neuromuscul Disord 2002; 12( Suppl 1): S169-S174.
    • (2002) Neuromuscul Disord , vol.12 , Issue.SUPPL. 1
    • Kinali, M.1    Mercuri, E.2    Main, M.3    Muntoni, F.4    Dubowitz, V.5
  • 16
    • 0034257910 scopus 로고    scopus 로고
    • Preserving function in Duchenne dystrophy with long-term pulse prednisone therapy
    • Carter GT, McDonald CM. Preserving function in Duchenne dystrophy with long-term pulse prednisone therapy. Am J Phys Med Rehabil 2000; 79: 455-458.
    • (2000) Am J Phys Med Rehabil , vol.79 , pp. 455-458
    • Carter, G.T.1    McDonald, C.M.2
  • 18
    • 0030912103 scopus 로고    scopus 로고
    • 47th ENMC International Workshop: Treatment of Muscular Dystrophy. 13-15 December 1996, Naarden, The Netherlands
    • Angelini C, Bonifati M, Dubowitz V, Henriksson K, Malaspina E, Merlini L, et al. 47th ENMC International Workshop: Treatment of Muscular Dystrophy. 13-15 December 1996, Naarden, The Netherlands. Neuromuscul Disord 1997; 7: 261-267.
    • (1997) Neuromuscul Disord , vol.7 , pp. 261-267
    • Angelini, C.1    Bonifati, M.2    Dubowitz, V.3    Henriksson, K.4    Malaspina, E.5    Merlini, L.6
  • 19
  • 20
    • 0033812726 scopus 로고    scopus 로고
    • A multicenter, double-blind, randomized trial of deflazacort versus prednisone in Duchenne muscular dystrophy
    • Bonifati MD, Ruzza G, Bonometto P, Berardinelli A, Gorni K, Orcesi S, et al. A multicenter, double-blind, randomized trial of deflazacort versus prednisone in Duchenne muscular dystrophy. Muscle Nerve 2000; 23: 1344-1347.
    • (2000) Muscle Nerve , vol.23 , pp. 1344-1347
    • Bonifati, M.D.1    Ruzza, G.2    Bonometto, P.3    Berardinelli, A.4    Gorni, K.5    Orcesi, S.6
  • 22
    • 0036307964 scopus 로고    scopus 로고
    • Reliability of hand-held dynamometry in spinal muscular atrophy
    • Merlini L, Mazzone ES, Solari A, Morandi L. Reliability of hand-held dynamometry in spinal muscular atrophy. Muscle Nerve 2002; 26: 64-70.
    • (2002) Muscle Nerve , vol.26 , pp. 64-70
    • Merlini, L.1    Mazzone, E.S.2    Solari, A.3    Morandi, L.4
  • 24
    • 0003556467 scopus 로고
    • Radiographic atlas of skeletal development of the hand and wrist
    • Stanford University Press: Stanford University Press;
    • Greulich WW, Pyle S. Radiographic atlas of skeletal development of the hand and wrist. California: Stanford University Press: Stanford University Press; 1950.
    • (1950) California
    • Greulich, W.W.1    Pyle, S.2
  • 25
    • 76549130473 scopus 로고    scopus 로고
    • Diagnosis and management of Duchenne muscular dystrophy, part 2: implementation of multidisciplinary care
    • Bushby K, Finkel R, Birnkrant DJ, Case LE, Clemens PR, Cripe L, et al. Diagnosis and management of Duchenne muscular dystrophy, part 2: implementation of multidisciplinary care. Lancet Neurol 2010; 9: 177-189.
    • (2010) Lancet Neurol , vol.9 , pp. 177-189
    • Bushby, K.1    Finkel, R.2    Birnkrant, D.J.3    Case, L.E.4    Clemens, P.R.5    Cripe, L.6
  • 26
    • 0012925987 scopus 로고    scopus 로고
    • Long-term steroid therapy in Duchenne muscular dystrophy-positive results versus side effects
    • Schara U, Mortier, Mortier W. Long-term steroid therapy in Duchenne muscular dystrophy-positive results versus side effects. J Clin Neuromuscul Dis 2001; 2: 179-183.
    • (2001) J Clin Neuromuscul Dis , vol.2 , pp. 179-183
    • Schara, U.1    Mortier2    Mortier, W.3
  • 28
    • 0036893708 scopus 로고    scopus 로고
    • High dose weekly oral prednisone improves strength in boys with Duchenne muscular dystrophy
    • Connolly AM, Schierbecker J, Renna R, Florence J. High dose weekly oral prednisone improves strength in boys with Duchenne muscular dystrophy. Neuromuscul Disord 2002; 12: 917-925.
    • (2002) Neuromuscul Disord , vol.12 , pp. 917-925
    • Connolly, A.M.1    Schierbecker, J.2    Renna, R.3    Florence, J.4
  • 29
    • 0019432012 scopus 로고
    • Respiratory function in the muscular dystrophies
    • Rideau Y, Jankowski LW, Grellet J. Respiratory function in the muscular dystrophies. Muscle Nerve 1981; 4: 155-164.
    • (1981) Muscle Nerve , vol.4 , pp. 155-164
    • Rideau, Y.1    Jankowski, L.W.2    Grellet, J.3
  • 30
    • 0025317772 scopus 로고
    • Decline in respiratory function and experience with long-term assisted ventilation in advanced Duchenne's muscular dystrophy
    • Baydur A, Gilgoff I, Prentice W, Carlson M, Fischer DA. Decline in respiratory function and experience with long-term assisted ventilation in advanced Duchenne's muscular dystrophy. Chest 1990; 97: 884-889.
    • (1990) Chest , vol.97 , pp. 884-889
    • Baydur, A.1    Gilgoff, I.2    Prentice, W.3    Carlson, M.4    Fischer, D.A.5
  • 31
    • 0036532426 scopus 로고    scopus 로고
    • Prognostic value of electrocardiograms, ventricular late potentials, ventricular arrhythmias, and left ventricular systolic dysfunction in patients with Duchenne muscular dystrophy
    • Corrado G, Lissoni A, Beretta S, Terenghi L, Tadeo G, Foglia-Manzillo G, et al. Prognostic value of electrocardiograms, ventricular late potentials, ventricular arrhythmias, and left ventricular systolic dysfunction in patients with Duchenne muscular dystrophy. Am J Cardiol 2002; 89: 838-841.
    • (2002) Am J Cardiol , vol.89 , pp. 838-841
    • Corrado, G.1    Lissoni, A.2    Beretta, S.3    Terenghi, L.4    Tadeo, G.5    Foglia-Manzillo, G.6
  • 32
    • 0037443583 scopus 로고    scopus 로고
    • Effects of deflazacort on left ventricular function in patients with Duchenne muscular dystrophy
    • Silversides CK, Webb GD, Harris VA, Biggar DW. Effects of deflazacort on left ventricular function in patients with Duchenne muscular dystrophy. Am J Cardiol 2003; 91: 769-772.
    • (2003) Am J Cardiol , vol.91 , pp. 769-772
    • Silversides, C.K.1    Webb, G.D.2    Harris, V.A.3    Biggar, D.W.4
  • 34
    • 77957753154 scopus 로고    scopus 로고
    • 170th ENMC International Workshop: Bone protection for corticosteroid treated Duchenne muscular dystrophy. 27-29 November 2009, Naarden, The Netherlands
    • Quinlivan R, Shaw N, Bushby K. 170th ENMC International Workshop: Bone protection for corticosteroid treated Duchenne muscular dystrophy. 27-29 November 2009, Naarden, The Netherlands. Neuromuscul Disord 2010; 20: 761-769.
    • (2010) Neuromuscul Disord , vol.20 , pp. 761-769
    • Quinlivan, R.1    Shaw, N.2    Bushby, K.3
  • 38
    • 0014736650 scopus 로고
    • Variations in the pattern of pubertal changes in boys
    • Marshall WA, Tanner JM. Variations in the pattern of pubertal changes in boys. Arch Dis Child 1970; 45: 13-23.
    • (1970) Arch Dis Child , vol.45 , pp. 13-23
    • Marshall, W.A.1    Tanner, J.M.2
  • 39
    • 0036896643 scopus 로고    scopus 로고
    • Body fat percentages measured by dual-energy X-ray absorptiometry corresponding to recently recommended body mass index cutoffs for overweight and obesity in children and adolescents aged 3-18 y
    • Taylor RW, Jones IE, Williams SM, Goulding A. Body fat percentages measured by dual-energy X-ray absorptiometry corresponding to recently recommended body mass index cutoffs for overweight and obesity in children and adolescents aged 3-18 y. Am J Clin Nutr 2002; 76: 1416-1421.
    • (2002) Am J Clin Nutr , vol.76 , pp. 1416-1421
    • Taylor, R.W.1    Jones, I.E.2    Williams, S.M.3    Goulding, A.4
  • 40
    • 34848840925 scopus 로고    scopus 로고
    • The role of corticosteroids in muscular dystrophy: a critical appraisal
    • Angelini C. The role of corticosteroids in muscular dystrophy: a critical appraisal. Muscle Nerve 2007; 36: 424-435.
    • (2007) Muscle Nerve , vol.36 , pp. 424-435
    • Angelini, C.1
  • 43
    • 0025869545 scopus 로고
    • Prednisone in Duchenne dystrophy. A randomized, controlled trial defining the time course and dose response. Clinical Investigation of Duchenne Dystrophy Group
    • Griggs RC, Moxley RT III, Mendell JR, Fenichel GM, Brooke MH, Pestronk A, et al. Prednisone in Duchenne dystrophy. A randomized, controlled trial defining the time course and dose response. Clinical Investigation of Duchenne Dystrophy Group. Arch Neurol 1991; 48: 383-388.
    • (1991) Arch Neurol , vol.48 , pp. 383-388
    • Griggs, R.C.1    Moxley III, R.T.2    Mendell, J.R.3    Fenichel, G.M.4    Brooke, M.H.5    Pestronk, A.6
  • 44
    • 0029011230 scopus 로고
    • Low-dose prednisolone treatment in Duchenne and Becker muscular dystrophy
    • Backman E, Henriksson KG. Low-dose prednisolone treatment in Duchenne and Becker muscular dystrophy. Neuromuscul Disord 1995; 5: 233-241.
    • (1995) Neuromuscul Disord , vol.5 , pp. 233-241
    • Backman, E.1    Henriksson, K.G.2
  • 46
    • 84860900166 scopus 로고    scopus 로고
    • P3.51 Results of a Phase 2b, dose-ranging study of ataluren (PTC124®) in nonsense mutation Duchenne/Becker muscular dystrophy (nmDBMD)
    • Finkel R, Wong B, Bushby K, Reha A, Elfring GL, Miller LL, et al. P3.51 Results of a Phase 2b, dose-ranging study of ataluren (PTC124®) in nonsense mutation Duchenne/Becker muscular dystrophy (nmDBMD). Neuromuscular Disorders 2010; 20: 656-657.
    • (2010) Neuromuscular Disorders , vol.20 , pp. 656-657
    • Finkel, R.1    Wong, B.2    Bushby, K.3    Reha, A.4    Elfring, G.L.5    Miller, L.L.6


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.