Novel cationic carotenoid lipids as delivery vectors of antisense oligonucleotides for exon skipping in duchenne muscular dystrophy

Molecules

Volumn 17, Issue 2, 2012, Pages 1138-1148

  Popplewell, Linda J ^a   Abu Dayya, Aseel ^b   Khanna, Tushar ^b   Flinterman, Marcella ^b   Khalique, Nada Abdul ^b   Raju, Liji ^b   Øpstad, Christer L ^c   Sliwka, Hans Richard ^c   Partali, Vassilia ^c   Dickson, George ^a   Pungente, Michael D ^b  

^a UNIVERSITY OF LONDON   (United Kingdom)

^b WEILL CORNELL MEDICAL COLLEGE   (Qatar)

^c NORWEGIAN UNIVERSITY OF SCIENCE AND TECHNOLOGY   (Norway)

Author keywords

Antisense oligonucleotide; Carotenoid; Cationic lipid; Duchenne muscular dystrophy; Exon skipping

Indexed keywords

ANTISENSE OLIGONUCLEOTIDE; CAROTENOID; CATION; DRUG CARRIER; LIPID;

AGAR GEL ELECTROPHORESIS; ARTICLE; DUCHENNE MUSCULAR DYSTROPHY; EXON; GENETICS; HUMAN; METABOLISM; REVERSE TRANSCRIPTION POLYMERASE CHAIN REACTION; SKELETAL MUSCLE;

CAROTENOIDS; CATIONS; DRUG CARRIERS; ELECTROPHORESIS, AGAR GEL; EXONS; HUMANS; LIPIDS; MUSCLE, SKELETAL; MUSCULAR DYSTROPHY, DUCHENNE; OLIGONUCLEOTIDES, ANTISENSE; REVERSE TRANSCRIPTASE POLYMERASE CHAIN REACTION;

EID: 84857524678     PISSN: None     EISSN: 14203049     Source Type: Journal    
DOI: 10.3390/molecules17021138     Document Type: Article

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