Population pharmacokinetics and pharmacodynamics of cysteamine in nephropathic cystinosis patients

Orphanet Journal of Rare Diseases

Volumn 6, Issue 1, 2011, Pages

  Bouazza, Nam ^a,b   Tréluyer, Jean Marc ^a,b,c,d   Ottolenghi, Chris ^e   Urien, Saik ^a,b,d   Deschenes, Georges ^f   Ricquier, Daniel ^e   Niaudet, Patrick ^e   Chadefaux Vekemans, Bernadette ^e  

^a UNIVERSITÉ PARIS DESCARTES   (France)

^b Paris Descartes University   (France)

^c Hôpital Cochin Saint Vincent de Paul ^*  (France)

^d INSERM   (France)

^e HÔPITAL NECKER ENFANTS MALADES   (France)

^f HÔPITAL ROBERT DEBRÉ   (France)

Author keywords

cysteamine; cystinosis; pharmacodynamics; population pharmacokinetics

Indexed keywords

CYSTINE; MERCAPTAMINE; RADIOPROTECTIVE AGENT;

ADOLESCENT; ADULT; ARTICLE; CHILD; CONTROLLED STUDY; CYSTINOSIS; DRUG BLOOD LEVEL; HUMAN; INFANT; KIDNEY DISEASE; LEUKOCYTE; MAJOR CLINICAL STUDY; PRESCHOOL CHILD; SCHOOL CHILD; BLOOD; BODY WEIGHT; CLINICAL TRIAL; DOSE RESPONSE; FEMALE; MALE; NEPHROPATHIC CYSTINOSIS; NEPHROTIC SYNDROME; TREATMENT OUTCOME;

ADOLESCENT; ADULT; BODY WEIGHT; CHILD; CHILD, PRESCHOOL; CYSTEAMINE; CYSTINE; CYSTINOSIS; DOSE-RESPONSE RELATIONSHIP, DRUG; FEMALE; HUMANS; INFANT; MALE; NEPHROTIC SYNDROME; RADIATION-PROTECTIVE AGENTS; TREATMENT OUTCOME; YOUNG ADULT;

EID: 84155182910     PISSN: None     EISSN: 17501172     Source Type: Journal    
DOI: 10.1186/1750-1172-6-86     Document Type: Article

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