-
1
-
-
0003187521
-
Regulation (EC) no. 141/ 2000 of the European Parliament and the Council of 16 December 1999 on orphan medicinal products
-
L 18/1
-
Regulation (EC) no. 141/2000 of the European Parliament and the Council of 16 December 1999 on orphan medicinal products. Official J Eur Commun 2000; L 18/1
-
(2000)
Official J Eur Commun
-
-
-
3
-
-
77953354292
-
Budget impact analysis of orphan drugs in Belgium: Estimates from 2008 to 2013
-
Denis A, Mergaert L, Fostier C, et al. Budget impact analysis of orphan drugs in Belgium: estimates from 2008 to 2013. J Med Econ 2010; 13 (2): 295-301
-
(2010)
J Med Econ
, vol.13
, Issue.2
, pp. 295-301
-
-
Denis, A.1
Mergaert, L.2
Fostier, C.3
-
4
-
-
34247504244
-
Assessing the economic challenges posed by orphan drugs
-
DOI 10.1017/S0266462307051550, PII S0266462307051550
-
Drummond MF, Wilson DA, Kanavos P, et al. Assessing the economic challenges posed by orphan drugs. Int J Technol Assess Health Care 2007; 23 (1): 36-42 (Pubitemid 46648298)
-
(2007)
International Journal of Technology Assessment in Health Care
, vol.23
, Issue.1
, pp. 36-42
-
-
Drummond, M.F.1
Wilson, D.A.2
Kanavos, P.3
Ubel, P.4
Rovira, J.5
-
5
-
-
76949104143
-
Factors associated with success of market authorisation applications for pharmaceutical drugs submitted to the European Medicines Agency
-
Regnstrom J, Koenig F, Aronsson B, et al. Factors associated with success of market authorisation applications for pharmaceutical drugs submitted to the European Medicines Agency. Eur J Clin Pharmacol 2010; 66 (1): 39-48
-
(2010)
Eur J Clin Pharmacol
, vol.66
, Issue.1
, pp. 39-48
-
-
Regnstrom, J.1
Koenig, F.2
Aronsson, B.3
-
6
-
-
41249093220
-
Exploring emerging technologies using metaphors: A study of orphan drugs and pharmacogenomics
-
Boon W, Moors E. Exploring emerging technologies using metaphors: a study of orphan drugs and pharmacogenomics. Soc Sci Med 2008; 66 (9): 1915-27
-
(2008)
Soc Sci Med
, vol.66
, Issue.9
, pp. 1915-27
-
-
Boon, W.1
Moors, E.2
-
7
-
-
79960196412
-
Drugs for rare diseases: Orphan designation status influences price
-
Picavet E, Dooms M, Cassiman D, et al. Drugs for rare diseases: orphan designation status influences price. Appl Health Econ Health Policy 2011; 9 (4): 1-5
-
(2011)
Appl Health Econ Health Policy
, vol.9
, Issue.4
, pp. 1-5
-
-
Picavet, E.1
Dooms, M.2
Cassiman, D.3
-
8
-
-
0021145218
-
Treatment of Lambert-Eaton syndrome: 3,4-diaminopyridine and pyridostigmine
-
Lundh H, Nilsson O, Rosen I. Treatment of Lambert-Eaton syndrome: 3,4-diaminopyridine and pyridostigmine. Neurology 1984; 34 (10): 1324-30 (Pubitemid 14047242)
-
(1984)
Neurology
, vol.34
, Issue.10
, pp. 1324-1330
-
-
Lundh, H.1
Nilsson, O.2
Rosen, I.3
-
10
-
-
0031907582
-
Intraoperative detection of malignant gliomas by 5-aminolevulinic acid-induced porphyrin fluorescence
-
Stummer W, Stocker S, Wagner S, et al. Intraoperative detection of malignant gliomas by 5-aminolevulinic acid-induced porphyrin fluorescence. Neurosurgery 1998; 42 (3): 518-25
-
(1998)
Neurosurgery
, vol.42
, Issue.3
, pp. 518-25
-
-
Stummer, W.1
Stocker, S.2
Wagner, S.3
-
11
-
-
0019406681
-
The use of betaine for the treatment of homocystinuria
-
DOI 10.1016/S0022-3476(81)80352-6
-
Smolin LA, Benevenga NJ, Berlow S. The use of betaine for the treatment of homocystinuria. J Pediatr 1981; 99 (3): 467-72 (Pubitemid 11029956)
-
(1981)
Journal of Pediatrics
, vol.99
, Issue.3
, pp. 467-472
-
-
Smolin, L.A.1
Benevenga, N.J.2
Berlow, S.3
-
12
-
-
0018081810
-
Cysteamine therapy for cystinosis
-
Roy LP, Pollard AC. Cysteamine therapy for cystinosis. Lancet 1978; II (8092 Pt 1): 729-30 (Pubitemid 9040750)
-
(1978)
Lancet
, vol.2
, Issue.8092
, pp. 729-730
-
-
Roy, L.P.1
Pollard, A.C.2
-
13
-
-
0025131042
-
Episodic hyperammonemia in adult siblings with hyperornithinemia, hyperammonemia, and homocitrullinuria syndrome
-
Tuchman M, Knopman DS, Shih VE. Episodic hyperammonemia in adult siblings with hyperornithinemia, hyperammonemia, and homocitrullinuria syndrome. Arch Neurol 1990; 47 (10): 1134-7 (Pubitemid 20326674)
-
(1990)
Archives of Neurology
, vol.47
, Issue.10
, pp. 1134-1137
-
-
Tuchman, M.1
Knopman, D.S.2
Shih, V.E.3
-
15
-
-
22144477549
-
Adopting an orphan
-
DOI 10.1038/sj.embor.7400450
-
Rinaldi A. Adopting an orphan. EMBO Rep 2005; 6 (6): 507-10. (Pubitemid 40973956)
-
(2005)
EMBO Reports
, vol.6
, Issue.6
, pp. 507-510
-
-
Rinaldi, A.1
|