Antisense Oligo-Mediated Multiple Exon Skipping in a Dog Model of Duchenne Muscular Dystrophy

Methods in Molecular Biology

Volumn 709, Issue , 2011, Pages 299-312

  Yokota, Toshifumi ^a   Hoffman, Eric ^a   Takeda, Shin’ichi ^b  

^a CHILDREN'S NATIONAL MEDICAL CENTER   (United States)

^b NATIONAL INSTITUTE OF NEUROSCIENCE   (Japan)

Author keywords

2 O methylated antisense oligomers (phosphorothioate); Duchenne Becker muscular dystrophies; Dystrophic dogs (canine X linked muscular dystrophy); Morpholinos (phosphorodiamidate morpholino oligomers); Multiple exon skipping

Indexed keywords

ANTISENSE OLIGONUCLEOTIDE; DYSTROPHIN; MORPHOLINE DERIVATIVE; PHOSPHORODIAMIDATE MORPHOLINO OLIGOMER;

ALTERNATIVE RNA SPLICING; ANIMAL; ANIMAL MUSCULAR DYSTROPHY; ARTICLE; DISEASE MODEL; DOG; DUCHENNE MUSCULAR DYSTROPHY; EXON; GENE THERAPY; GENETICS; METHODOLOGY; NUCLEOTIDE SEQUENCE; PHENOTYPE; SKELETAL MUSCLE;

ALTERNATIVE SPLICING; ANIMALS; DISEASE MODELS, ANIMAL; DOGS; DYSTROPHIN; EXONS; GENE THERAPY; MORPHOLINES; MUSCLE, SKELETAL; MUSCULAR DYSTROPHY, ANIMAL; MUSCULAR DYSTROPHY, DUCHENNE; OLIGONUCLEOTIDES, ANTISENSE; PHENOTYPE; READING FRAMES;

EID: 79960055339     PISSN: 10643745     EISSN: 19406029     Source Type: Book Series    
DOI: 10.1007/978-1-61737-982-6_20     Document Type: Chapter

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