Engineering Exon-Skipping Vectors Expressing U7 snRNA Constructs for Duchenne Muscular Dystrophy Gene Therapy

Methods in Molecular Biology

Volumn 709, Issue , 2011, Pages 179-196

  Goyenvalle, Aurélie ^a   Davies, Kay E ^a  

^a UNIVERSITY OF OXFORD   (United Kingdom)

Author keywords

AAV vector; Antisense; Duchenne muscular dystrophy; Exon skipping; Exonic splicing silencer; Gene therapy; Lentiviral vector; U7 snRNA

Indexed keywords

COMPLEMENTARY DNA; DYSTROPHIN; HETEROGENEOUS NUCLEAR RIBONUCLEOPROTEIN; HNRNP A1; SMALL NUCLEAR RNA; U7 SMALL NUCLEAR RNA;

ADENO ASSOCIATED VIRUS; ALTERNATIVE RNA SPLICING; ANIMAL; ARTICLE; DUCHENNE MUSCULAR DYSTROPHY; GENE EXPRESSION; GENE THERAPY; GENE TRANSFER; GENE VECTOR; GENETIC ENGINEERING; GENETICS; HUMAN; METABOLISM; METHODOLOGY; MOUSE; NUCLEOTIDE SEQUENCE; TRANSGENIC MOUSE;

ALTERNATIVE SPLICING; ANIMALS; DEPENDOVIRUS; DNA, ANTISENSE; DYSTROPHIN; GENE EXPRESSION; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC ENGINEERING; GENETIC VECTORS; HETEROGENEOUS-NUCLEAR RIBONUCLEOPROTEIN GROUP A-B; HUMANS; MICE; MICE, TRANSGENIC; MUSCULAR DYSTROPHY, DUCHENNE; READING FRAMES; RNA, SMALL NUCLEAR;

EID: 79960052376     PISSN: 10643745     EISSN: 19406029     Source Type: Book Series    
DOI: 10.1007/978-1-61737-982-6_11     Document Type: Chapter

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