Laronidase replacement therapy improves myocardial function in mucopolysaccharidosis I

Molecular Genetics and Metabolism

Volumn 103, Issue 3, 2011, Pages 215-219

  Harada, Haruhito ^a   Uchiwa, Hiroki ^a   Nakamura, Mio ^a   Ohno, Satoko ^a   Morita, Hirohiko ^a   Katoh, Atsushi ^a   Yoshino, Makoto ^b   Ikeda, Hisao ^a  

^a KURUME UNIVERSITY MEDICAL CENTER   (Japan)

^b KURUME UNIVERSITY SCHOOL OF MEDICINE   (Japan)

Author keywords

Laronidase replacement therapy; Mucopolysaccharidosis I; Myocardial function; Speckle tracking imaging

Indexed keywords

AMLODIPINE; CANDESARTAN; CARVEDILOL; CIBENZOLINE; LARONIDASE; WARFARIN;

ADULT; AORTA VALVE REGURGITATION; ARTICLE; CASE REPORT; CONGESTIVE HEART FAILURE; ENZYME REPLACEMENT; FEMALE; HEART ATRIUM FIBRILLATION; HEART FAILURE; HEART FUNCTION; HEART LEFT VENTRICLE EJECTION FRACTION; HEART LEFT VENTRICLE FUNCTION; HEART LEFT VENTRICLE MASS; HEART VALVE REPLACEMENT; HEPATOSPLENOMEGALY; HUMAN; HURLER SYNDROME; MITRAL VALVE REGURGITATION; PRIORITY JOURNAL; TWO DIMENSIONAL ECHOCARDIOGRAPHY;

ENZYME REPLACEMENT THERAPY; FEMALE; HEART VENTRICLES; HUMANS; IDURONIDASE; LIVER; MIDDLE AGED; MUCOPOLYSACCHARIDOSIS I; ORGAN SIZE; SPLEEN; TIME FACTORS; TREATMENT OUTCOME;

EID: 79958064052     PISSN: 10967192     EISSN: 10967206     Source Type: Journal    
DOI: 10.1016/j.ymgme.2011.03.016     Document Type: Article

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