-
1
-
-
79957890386
-
Engineering liver-detargeted AAV9 vectors for cardiac and musculoskeletal gene transfer
-
Pulicherla, N, Shen, S, Yadav, S, Debbink, K, Gov-indasamy, L, Agbandje-McKenna, M et al. (2011). Engineering liver-detargeted AAV9 vectors for cardiac and musculoskeletal gene transfer. Mol Ther 19: 1070-1078.
-
(2011)
Mol Ther
, vol.19
, pp. 1070-1078
-
-
Pulicherla, N.1
Shen, S.2
Yadav, S.3
Debbink, K.4
Gov-Indasamy, L.5
Agbandje-Mckenna, M.6
-
2
-
-
40549119871
-
Designer gene delivery vectors: Molecular engineering and evolution of adeno-associated viral vectors for enhanced gene transfer
-
Kwon, I and Schaffer, DV (2008). Designer gene delivery vectors: molecular engineering and evolution of adeno-associated viral vectors for enhanced gene transfer. Pharm Res 25: 489-499.
-
(2008)
Pharm Res
, vol.25
, pp. 489-499
-
-
Kwon, I.1
Schaffer, D.V.2
-
3
-
-
1342268978
-
Development of efficient viral vectors selective for vascular smooth muscle cells
-
DOI 10.1016/j.ymthe.2003.11.006
-
Work, LM, Nicklin, SA, Brain, NJ, Dishart, KL, Von Seggem, DJ, Hallek, M et al. (2004). Development of effcient viral vectors selective for vascular smooth muscle cells. Mol Ther 9: 198-208. (Pubitemid 38256546)
-
(2004)
Molecular Therapy
, vol.9
, Issue.2
, pp. 198-208
-
-
Work, L.M.1
Nicklin, S.A.2
Brain, N.J.R.3
Dishart, K.L.4
Von Seggern, D.J.5
Hallek, M.6
Buning, H.7
Baker, A.H.8
-
4
-
-
79957888016
-
Preclinical differences of intravascular AAV9 delivery to neurons and glia: A comparative study of adult mice and nonhuman primates
-
Gray, SJ, Matagne, V, Bachaboina, L, Yadav, S, Ojeda, SR, Samulski, RJ (2011). Preclinical differences of intravascular AAV9 delivery to neurons and glia: a comparative study of adult mice and nonhuman primates. Mol Ther 19: 1058-1069.
-
(2011)
Mol Ther
, vol.19
, pp. 1058-1069
-
-
Gray, S.J.1
Matagne, V.2
Bachaboina, L.3
Yadav, S.4
Ojeda, S.R.5
Samulski, R.J.6
-
5
-
-
0034050904
-
Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector
-
DOI 10.1038/73464
-
Kay, MA, Manno, CS, Ragni, MV, Larson, PJ, Couto, LB, McClelland, A et al. (2000). Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector. Nat Genet 24: 257-261. (Pubitemid 30132193)
-
(2000)
Nature Genetics
, vol.24
, Issue.3
, pp. 257-261
-
-
Kay, M.A.1
Manno, C.S.2
Ragni, M.V.3
Larson, P.J.4
Couto, L.B.5
McClelland, A.6
Glader, B.7
Chew, A.J.8
Tai, S.J.9
Herzog, R.W.10
Arruda, V.11
Johnson, F.12
Scallan, C.13
Skarsgard, E.14
Flake, A.W.15
High, K.A.16
-
6
-
-
37549059628
-
Current status of gene therapy trials for Parkinson's disease
-
Fiandaca, M, Forsayeth, J and Bankiewicz, K (2008). Current status of gene therapy trials for Parkinson's disease. Exp Neurol 209: 51-57.
-
(2008)
Exp Neurol
, vol.209
, pp. 51-57
-
-
Fiandaca, M.1
Forsayeth, J.2
Bankiewicz, K.3
-
7
-
-
2642512201
-
Clades of adeno-associated viruses are widely disseminated in human tissues
-
DOI 10.1128/JVI.78.12.6381-6388.2004
-
Gao, G, Vandenberghe, LH, Alvira, MR, Lu, Y, Calcedo, R, Zhou, X et al. (2004). Clades of adeno-associated viruses are widely disseminated in human tissues. J Virol 78: 6381-6388. (Pubitemid 38715936)
-
(2004)
Journal of Virology
, vol.78
, Issue.12
, pp. 6381-6388
-
-
Gao, G.1
Vandenberghe, L.H.2
Alvira, M.R.3
Lu, Y.4
Calcedo, R.5
Zhou, X.6
Wilson, J.M.7
-
8
-
-
54749126318
-
Expanded repertoire of AAV vector serotypes mediate unique patterns of transduction in mouse brain
-
Cearley, CN, Vandenberghe, LH, Parente, MK, Car-nish, ER, Wilson, JM and Wolfe, JH (2008). Expanded repertoire of AAV vector serotypes mediate unique patterns of transduction in mouse brain. Mol Ther 16: 1710-1718.
-
(2008)
Mol Ther
, vol.16
, pp. 1710-1718
-
-
Cearley, C.N.1
Vandenberghe, L.H.2
Parente, M.K.3
Car-Nish, E.R.4
Wilson, J.M.5
Wolfe, J.H.6
-
9
-
-
61649101243
-
AAV9: A potential blood-brain barrier buster
-
Manfredsson, F P, Rising, AC and Mandel, RJ (2009). AAV9: a potential blood-brain barrier buster. Mol Ther 17: 403-405.
-
(2009)
Mol Ther
, vol.17
, pp. 403-405
-
-
Manfredsson, F.P.1
Rising, A.C.2
Mandel, R.J.3
-
10
-
-
79957882063
-
Correction of neurological disease of mucopoly-saccharidosis IIIB in adult mice by rAAV9 trans-blood-brain barrier gene delivery
-
Fu, H, DiRosario, J, Killedar, S, Zaraspe, K, McCarty, DM (2011). Correction of neurological disease of mucopoly-saccharidosis IIIB in adult mice by rAAV9 trans-blood-brain barrier gene delivery. Mol Ther 19: 1025-1033.
-
(2011)
Mol Ther
, vol.19
, pp. 1025-1033
-
-
Fu, H.1
Dirosario, J.2
Killedar, S.3
Zaraspe, K.4
McCarty, D.M.5
-
11
-
-
60149106907
-
Intravascular AAV9 preferentially targets neonatal neurons and adult astro-cytes
-
Foust, KD, Nurre, E, Montgomery, CL, Hernandez, A, Chan, CM and Kaspar, BK (2009). Intravascular AAV9 preferentially targets neonatal neurons and adult astro-cytes. Nat Biotechnol 27: 59-65.
-
(2009)
Nat Biotechnol
, vol.27
, pp. 59-65
-
-
Foust, K.D.1
Nurre, E.2
Montgomery, C.L.3
Hernandez, A.4
Chan, C.M.5
Kaspar, B.K.6
-
12
-
-
73449122430
-
Safety evaluation of AAV2-GDNF gene transfer into the dopaminergic nigrostriatal pathway in aged and parkinsonian rhesus monkeys
-
Su, X, Kells, A P, Huang, EJ, Lee, HS, Hadaczek, P, Bever, J et al. (2009). Safety evaluation of AAV2-GDNF gene transfer into the dopaminergic nigrostriatal pathway in aged and parkinsonian rhesus monkeys. Hum Gene Ther 20: 1627-1640.
-
(2009)
Hum Gene Ther
, vol.20
, pp. 1627-1640
-
-
Su, X.1
Kells, A.P.2
Huang, E.J.3
Lee, H.S.4
Hadaczek, P.5
Bever, J.6
-
13
-
-
67349113221
-
Nigrostriatal rAAV-mediated GDNF overexpression induces robust weight loss in a rat model of age-related obesity
-
Manfredsson, F P, Tumer, N, Erdos, B, Landa, T, Broxson, CS, Sullivan, LF et al. (2009). Nigrostriatal rAAV-mediated GDNF overexpression induces robust weight loss in a rat model of age-related obesity. Mol Ther 17: 980-991.
-
(2009)
Mol Ther
, vol.17
, pp. 980-991
-
-
Manfredsson, F.P.1
Tumer, N.2
Erdos, B.3
Landa, T.4
Broxson, C.S.5
Sullivan, L.F.6
-
14
-
-
77954976233
-
Prevalence of serum IgG and neutralizing factors against adeno-associated virus (AAV) types 1, 2, 5, 6, 8, and 9 in the healthy population: Implications for gene therapy using AAV vectors
-
Boutin, S, Monteilhet, V, Veron, P, Leborgne, C, Benveniste, O, Montus, MF et al. (2010). Prevalence of serum IgG and neutralizing factors against adeno-associated virus (AAV) types 1, 2, 5, 6, 8, and 9 in the healthy population: implications for gene therapy using AAV vectors. Hum Gene Ther 21: 704-712.
-
(2010)
Hum Gene Ther
, vol.21
, pp. 704-712
-
-
Boutin, S.1
Monteilhet, V.2
Veron, P.3
Leborgne, C.4
Benveniste, O.5
Montus, M.F.6
-
15
-
-
0032853699
-
Immune responses to adenovirus and adeno-associated virus in humans
-
DOI 10.1038/sj.gt.3300994
-
Chirmule, N, Propert, K, Magosin, S, Qian, Y, Qian, R and Wilson, J (1999). Immune responses to adeno-virus and adeno-associated virus in humans. Gene Ther 6: 1574-1583. (Pubitemid 29465516)
-
(1999)
Gene Therapy
, vol.6
, Issue.9
, pp. 1574-1583
-
-
Chirmule, N.1
Propert, K.J.2
Magosin, S.A.3
Qian, Y.4
Qian, R.5
Wilson, J.M.6
-
16
-
-
33344466244
-
Human immunoglobulin inhibits liver transduction byAAV vectors at low AAV2 neutralizing titers in SCID mice
-
DOI 10.1182/blood-2005-08-3229
-
Scallan, CD, Jiang, H, Liu, T, Patarroyo-White, S, Sommer, JM, Zhou, S et al. (2006). Human immuno-globulin inhibits liver transduction by AAV vectors at low AAV2 neutralizing titers in SCID mice. Blood 107: 1810-1817. (Pubitemid 43289358)
-
(2006)
Blood
, vol.107
, Issue.5
, pp. 1810-1817
-
-
Scallan, C.D.1
Jiang, H.2
Liu, T.3
Patarroyo-White, S.4
Sommer, J.M.5
Zhou, S.6
Couto, L.B.7
Pierce, G.F.8
-
17
-
-
33645923713
-
Prevalence of neutralizing antibodies against adeno-associated virus (AAV) types 2, 5, and 6 in cystic fbrosis and normal populations: Implications for gene therapy using AAV vectors
-
Halbert, CL, Miller, AD, McNamara, S, Emerson, J, Gibson, RL, Ramsey, B et al. (2006). Prevalence of neutralizing antibodies against adeno-associated virus (AAV) types 2, 5, and 6 in cystic fbrosis and normal populations: implications for gene therapy using AAV vectors. Hum Gene Ther 17: 440-447.
-
(2006)
Hum Gene Ther
, vol.17
, pp. 440-447
-
-
Halbert, C.L.1
Miller, A.D.2
McNamara, S.3
Emerson, J.4
Gibson, R.L.5
Ramsey, B.6
-
18
-
-
68949220858
-
Producing recombinant adeno-associated virus in foster cells: Overcoming production limitations using a baculovirus-insect cell expression strategy
-
Virag, T, Cecchini, S and Kotin, RM (2009). Producing recombinant adeno-associated virus in foster cells: overcoming production limitations using a baculovirus-insect cell expression strategy. Hum Gene Ther 20: 807-817.
-
(2009)
Hum Gene Ther
, vol.20
, pp. 807-817
-
-
Virag, T.1
Cecchini, S.2
Kotin, R.M.3
|