Effects of enzyme replacement therapy on growth in patients with mucopolysaccharidosis type II

Journal of Inherited Metabolic Disease

Volumn 34, Issue 1, 2011, Pages 203-208

  Schulze Frenking, G ^a   Jones, Simon A ^b   Roberts, J ^b   Beck, M ^a   Wraith, J E ^b  

^a JOHANNES GUTENBERG UNIVERSITY   (Germany)

^b ST MARY S HOSPITAL   (United Kingdom)

Author keywords

[No Author keywords available]

Indexed keywords

IDURONATE 2 SULFATASE; PLACEBO;

ADOLESCENT; ADULT; ARTICLE; BODY HEIGHT; CHILD; CLINICAL ARTICLE; CONTROLLED STUDY; DRUG EFFECT; ENZYME REPLACEMENT; GERMANY; GROWTH CURVE; GROWTH RATE; HUMAN; HUNTER SYNDROME; MALE; PRESCHOOL CHILD; RETROSPECTIVE STUDY; SCHOOL CHILD; SHORT STATURE; UNITED KINGDOM; CHILD DEVELOPMENT; EVALUATION; PATHOPHYSIOLOGY; PHASE 2 CLINICAL TRIAL (TOPIC); PHASE 3 CLINICAL TRIAL (TOPIC); PHYSIOLOGY;

ADOLESCENT; ADULT; BODY HEIGHT; CHILD; CHILD DEVELOPMENT; CLINICAL TRIALS, PHASE II AS TOPIC; CLINICAL TRIALS, PHASE III AS TOPIC; ENZYME REPLACEMENT THERAPY; GROWTH CHARTS; HUMANS; IDURONATE SULFATASE; MALE; MUCOPOLYSACCHARIDOSIS II; PLACEBOS; YOUNG ADULT;

EID: 79955792706     PISSN: 01418955     EISSN: 15732665     Source Type: Journal    
DOI: 10.1007/s10545-010-9215-2     Document Type: Article

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