Adeno-associated virus serotype 8 gene transfer rescues a neonatal lethal murine model of propionic acidemia

Human Gene Therapy

Volumn 22, Issue 4, 2011, Pages 477-481

  Chandler, Randy J ^a,b   Chandrasekaran, Suma ^a   Carrillo Carrasco, Nuria ^a   Senac, Julien S ^a   Hofherr, Sean E ^c   Barry, Michael A ^d   Venditti, Charles P ^a  

^a NATIONAL HUMAN GENOME RESEARCH INSTITUTE   (United States)

^b GEORGE WASHINGTON UNIVERSITY SCHOOL OF MEDICINE AND HEALTH SCIENCES   (United States)

^c MAYO CLINIC   (United States)

^d Translational Immunovirology Program   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; COMPLEMENTARY DNA; LIVER EXTRACT;

ADENO ASSOCIATED VIRUS; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; DISEASE MARKER; ENZYME ACTIVITY; HUMAN; MOUSE; NONHUMAN; PROPIONIC ACIDEMIA; SEROTYPE; VIRAL GENE DELIVERY SYSTEM; WESTERN BLOTTING; WILD TYPE;

ANIMALS; CITRATES; DEPENDOVIRUS; DISEASE MODELS, ANIMAL; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; METHYLMALONYL-COA DECARBOXYLASE; MICE; MICE, INBRED C57BL; MICE, KNOCKOUT; PHENOTYPE; PROPIONIC ACIDEMIA; SURVIVAL ANALYSIS;

ADENO-ASSOCIATED VIRUS; ANIMALIA; MURINAE; MUS;

EID: 79954533921     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.2010.164     Document Type: Article

References (21)

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