메뉴 건너뛰기




Volumn 686, Issue , 2010, Pages 41-53

Evidence-based medicine and rare diseases

Author keywords

Bias; Bradford Hill; Evidence; Meta analysis; Patient preference; Precision

Indexed keywords

ARTICLE; DRUG RESEARCH; EVIDENCE BASED MEDICINE; HEALTH CARE ACCESS; HUMAN; INFORMATION PROCESSING; INFORMED CONSENT; INTERNATIONAL COOPERATION; MEDICAL INFORMATION; META ANALYSIS (TOPIC); OFF LABEL DRUG USE; PATIENT DECISION MAKING; PATIENT SAFETY; PRIORITY JOURNAL; QUALITY CONTROL; RANDOMIZED CONTROLLED TRIAL (TOPIC); RARE DISEASE; RELIABILITY; RISK ASSESSMENT; RISK BENEFIT ANALYSIS; SYSTEMATIC ERROR; EXPERT WITNESS; METHODOLOGY; PATIENT PREFERENCE; REVIEW; STANDARD; STATISTICS;

EID: 79952067025     PISSN: 00652598     EISSN: None     Source Type: Book Series    
DOI: 10.1007/978-90-481-9485-8_3     Document Type: Article
Times cited : (9)

References (32)
  • 2
    • 0014424054 scopus 로고
    • When should randomisation begin?
    • Chalmers TC (1968) When should randomisation begin? Lancet 1(7547):858
    • (1968) Lancet , vol.1 , Issue.7547 , pp. 858
    • Chalmers, T.C.1
  • 3
    • 0016730858 scopus 로고
    • Randomization of the first patient
    • Chalmers TC (1975) Randomization of the first patient. Med Clin North Am 59:1035-1038
    • (1975) Med Clin North Am , vol.59 , pp. 1035-1038
    • Chalmers, T.C.1
  • 4
    • 0017618424 scopus 로고
    • Randomize the first patient!
    • Chalmers TC (1977) Randomize the first patient! N Engl J Med 296:107
    • (1977) N Engl J Med , vol.296 , pp. 107
    • Chalmers, T.C.1
  • 5
    • 79959561973 scopus 로고    scopus 로고
    • Committee forMedicinal Products for Human Use (CHMP) (2006) Guideline on clinical trials in small populations. European Medicines Agency, London
    • Committee forMedicinal Products for Human Use (CHMP) (2006) Guideline on clinical trials in small populations. European Medicines Agency, London
  • 6
    • 79959573154 scopus 로고    scopus 로고
    • Bayesian statistics
    • Day S (2009) Bayesian statistics. DIA Global Forum 1(6):34-35
    • (2009) DIA Global Forum , vol.1 , Issue.6 , pp. 34-35
    • Day, S.1
  • 7
    • 0035338343 scopus 로고    scopus 로고
    • Risks in new drug development: Approval success rates for investigational drugs
    • DOI 10.1067/mcp.2001.115446
    • DiMasi JA (2001) Risks in new drug development: Approval success rates for investigational drugs. Clin Pharm Therap 69:297-307 (Pubitemid 32477070)
    • (2001) Clinical Pharmacology and Therapeutics , vol.69 , Issue.5 , pp. 297-307
    • DiMasi, J.A.1
  • 9
    • 3042651139 scopus 로고    scopus 로고
    • Grading quality of evidence and strength of association
    • GRADE Working Group
    • GRADE Working Group (2004) Grading quality of evidence and strength of association. Brit Med J 328:1490-1494
    • (2004) Brit Med J , vol.328 , pp. 1490-1494
  • 10
    • 0021741474 scopus 로고
    • Using observational data from registries to compare treatments: The fallacy of omnimetrics
    • Green SB, Byar DP (1984) Using observational data from registries to compare treatments: The fallacy of omnimetrics. Stat Med 3:361-370 (Pubitemid 15167910)
    • (1984) Statistics in Medicine , vol.3 , Issue.4 , pp. 361-370
    • Green, S.B.1    Byar, D.P.2
  • 11
    • 0009690966 scopus 로고
    • The clinical trial
    • Hill AB (1951) The clinical trial. Brit Med Bull 7:278-282
    • (1951) Brit Med Bull , vol.7 , pp. 278-282
    • Hill, A.B.1
  • 12
    • 31844443695 scopus 로고
    • The environment and disease: Association or causation?
    • Hill AB (1965) The environment and disease: Association or causation? Proc Roy Soc Med 58:295-300
    • (1965) Proc Roy Soc Med , vol.58 , pp. 295-300
    • Hill, A.B.1
  • 13
    • 4344645978 scopus 로고    scopus 로고
    • Can the pharmaceutical industry reduce attrition rates?
    • Kola I, Landis J (2004) Can the pharmaceutical industry reduce attrition rates? Nat Rev Drug Discov 3:711-715 (Pubitemid 39173511)
    • (2004) Nature Reviews Drug Discovery , vol.3 , Issue.8 , pp. 711-715
    • Kola, I.1    Landis, J.2
  • 15
    • 58149290041 scopus 로고    scopus 로고
    • Two per cent isn't a lot, but when it comes to death it seems quite a lot anyway": Patients' perception of risk and willingness to accept risks associated with thrombolytic drug treatment for acute stroke
    • Mangset M, Berge E, Fø rde R, Nessa J, Wyller TB (2009) "Two per cent isn't a lot, but when it comes to death it seems quite a lot anyway": Patients' perception of risk and willingness to accept risks associated with thrombolytic drug treatment for acute stroke. J Med Ethics 35:42-46
    • (2009) J Med Ethics , vol.35 , pp. 42-46
    • Mangset, M.1    Berge, E.2    Førde, R.3    Nessa, J.4    Wyller, T.B.5
  • 16
    • 0028848039 scopus 로고
    • Small clinical trials: Are they all bad?
    • Matthews JNS (1995) Small clinical trials: Are they all bad? Stat Med 14:115-126
    • (1995) Stat Med , vol.14 , pp. 115-126
    • Matthews, J.N.S.1
  • 18
    • 33746699651 scopus 로고    scopus 로고
    • Access before approval - A right to take experimental drugs?
    • DOI 10.1056/NEJMp068132
    • Okie S (2006) Access before approval - a right to take experimental drugs? N Engl J Med 355:437-440 (Pubitemid 44162269)
    • (2006) New England Journal of Medicine , vol.355 , Issue.5 , pp. 437-440
    • Okie, S.1
  • 19
    • 33845269380 scopus 로고    scopus 로고
    • The bitterest pill
    • Pearson H
    • Pearson H (2006) The bitterest pill. Nature 444:532-533
    • (2006) Nature , vol.444 , pp. 532-533
  • 20
    • 0034839284 scopus 로고    scopus 로고
    • The economics of 'more research is needed'
    • Phillips CV (2001) The economics of 'more research is needed'. Int J Epidem 30: 771-776
    • (2001) Int J Epidem , vol.30 , pp. 771-776
    • Phillips, C.V.1
  • 21
    • 0025166539 scopus 로고
    • Hazards of small clinical trials
    • Piantadosi S (1990) Editorial. Hazards of small clinical trials. J Clin Oncol 8:1-3 (Pubitemid 20032438)
    • (1990) Journal of Clinical Oncology , vol.8 , Issue.1 , pp. 1-3
    • Piantadosi, S.1
  • 23
    • 0023567330 scopus 로고
    • Should unevaluated therapies be available for sale?
    • Reidenberg MM (1987) Should unevaluated therapies be available for sale? Clin Pharmacol Ther 42:599-600 (Pubitemid 18025769)
    • (1987) Clinical Pharmacology and Therapeutics , vol.42 , Issue.6 , pp. 599-600
    • Reidenberg, M.M.1
  • 25
    • 0029010826 scopus 로고
    • Coping with an embarrassment of riches
    • Saver JL (1995) Coping with an embarrassment of riches. Stroke 26:1289-1292
    • (1995) Stroke , vol.26 , pp. 1289-1292
    • Saver, J.L.1
  • 27
    • 33645828754 scopus 로고    scopus 로고
    • The society for clinical trials opposes us legislation to permit marketing of unproven medical therapies for seriously ill patients
    • Society for Clinical Trials Board of Directors
    • Society for Clinical Trials Board of Directors (2006) The Society for Clinical Trials opposes US legislation to permit marketing of unproven medical therapies for seriously ill patients. Clin Trials 3:154-157
    • (2006) Clin Trials , vol.3 , pp. 154-157
  • 28
    • 0020695661 scopus 로고
    • Randomize the first patient: Scientific, ethical, and behavioral bases
    • Spodick DH (1983) Randomize the first patient: Scientific, ethical, and behavioral bases. Am J Cardiol 51:916-917 (Pubitemid 13141997)
    • (1983) American Journal of Cardiology , vol.51 , Issue.5 , pp. 916-917
    • Spodick, D.H.1
  • 31
    • 79959536513 scopus 로고    scopus 로고
    • Code of federal regulations 21 CFR 314.126
    • United States Department of Health and Human Services, fda.gov/scripts/cdrh/cfdocs/cfcfr/CFRSearch.cfm. Cited 31st December 2009
    • United States Department of Health and Human Services (2009) Code of Federal Regulations 21 CFR 314.126. Adequate and well controlled studies. http://www.accessdata.fda.gov/scripts/cdrh/cfdocs/cfcfr/CFRSearch.cfm. Cited 31st December 2009
    • (2009) Adequate and Well Controlled Studies


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.