-
1
-
-
4043092073
-
Systemic delivery of genes to striated muscles using adeno-associated viral vectors
-
Gregorevic P, Blankinship MJ, Allen JM, Crawford RW, Meuse L, et al. (2004) Systemic delivery of genes to striated muscles using adeno-associated viral vectors. Nat Med 10(8): 828-834.
-
(2004)
Nat Med
, vol.10
, Issue.8
, pp. 828-834
-
-
Gregorevic, P.1
Blankinship, M.J.2
Allen, J.M.3
Crawford, R.W.4
Meuse, L.5
-
2
-
-
27444434461
-
Sustained wholebody functional rescue in congestive heart failure and muscular dystrophy hamsters by systemic gene transfer
-
Zhu T, Zhou L, Mori S, Wang Z, McTiernan CF, et al. (2005) Sustained wholebody functional rescue in congestive heart failure and muscular dystrophy hamsters by systemic gene transfer. Circulation 112(17): 2650-2659.
-
(2005)
Circulation
, vol.112
, Issue.17
, pp. 2650-2659
-
-
Zhu, T.1
Zhou, L.2
Mori, S.3
Wang, Z.4
McTiernan, C.F.5
-
3
-
-
45549090635
-
Next generation of adeno-associated virus 2 vectors: Point mutations in tyrosines lead to high-efficiency transduction at lower doses
-
Zhong L, Li B, Mah CS, Govindasamy L, Agbandje-McKenna M, et al. (2008) Next generation of adeno-associated virus 2 vectors: point mutations in tyrosines lead to high-efficiency transduction at lower doses. Proc Natl Acad Sci U S A 105(22): 7827-7832.
-
(2008)
Proc Natl Acad Sci U S A
, vol.105
, Issue.22
, pp. 7827-7832
-
-
Zhong, L.1
Li, B.2
Mah, C.S.3
Govindasamy, L.4
Agbandje-McKenna, M.5
-
4
-
-
61649095399
-
Highefficiency transduction of the mouse retina by tyrosine-mutant AAV serotype vectors
-
Petrs-Silva H, Dinculescu A, Li Q, Min SH, Chiodo V, et al. (2009) Highefficiency transduction of the mouse retina by tyrosine-mutant AAV serotype vectors. Mol Ther 17(3): 463-471.
-
(2009)
Mol Ther
, vol.17
, Issue.3
, pp. 463-471
-
-
Petrs-Silva, H.1
Dinculescu, A.2
Li, Q.3
Min, S.H.4
Chiodo, V.5
-
5
-
-
78650898983
-
Highefficiency transduction and correction of murine hemophilia B using AAV2 vectors devoid of multiple surface-exposed tyrosines
-
[Epub ahead of print]
-
Markusic DM, Herzog RW, Aslanidi GV, Hoffman BE, Li B, et al. (2010) Highefficiency transduction and correction of murine hemophilia B using AAV2 vectors devoid of multiple surface-exposed tyrosines. Mol Ther [Epub ahead of print].
-
(2010)
Mol Ther
-
-
Markusic, D.M.1
Herzog, R.W.2
Aslanidi, G.V.3
Hoffman, B.E.4
Li, B.5
-
6
-
-
73249123039
-
Engineering adeno-associated virus serotype 2-based targeting vectors using a new insertion site-position 453-and single point mutations
-
Boucas J, Lux K, Huber A, Schievenbusch S, von Freyend MJ, et al. (2009) Engineering adeno-associated virus serotype 2-based targeting vectors using a new insertion site-position 453-and single point mutations. J Gene Med 11(12): 1103-1113.
-
(2009)
J Gene Med
, vol.11
, Issue.12
, pp. 1103-1113
-
-
Boucas, J.1
Lux, K.2
Huber, A.3
Schievenbusch, S.4
von Freyend, M.J.5
-
7
-
-
69249213448
-
A muscle-targeting peptide displayed on AAV2 improves muscle tropism on systemic delivery
-
Yu CY, Yuan Z, Cao Z, Wang B, Qiao C, et al. (2009) A muscle-targeting peptide displayed on AAV2 improves muscle tropism on systemic delivery. Gene Ther 16(8): 953-962.
-
(2009)
Gene Ther
, vol.16
, Issue.8
, pp. 953-962
-
-
Yu, C.Y.1
Yuan, Z.2
Cao, Z.3
Wang, B.4
Qiao, C.5
-
8
-
-
62649151797
-
A myocardium tropic adeno-associated virus (AAV) evolved by DNA shuffling and in vivo selection
-
Yang L, Jiang J, Drouin LM, Agbandje-McKenna M, Chen C, et al. (2009) A myocardium tropic adeno-associated virus (AAV) evolved by DNA shuffling and in vivo selection. Proc Natl Acad Sci U S A 106(10): 3946-3951.
-
(2009)
Proc Natl Acad Sci U S A
, vol.106
, Issue.10
, pp. 3946-3951
-
-
Yang, L.1
Jiang, J.2
Drouin, L.M.3
Agbandje-McKenna, M.4
Chen, C.5
-
9
-
-
0033987131
-
Incorporation of adenoassociated virus in a calcium phosphate coprecipitate improves gene transfer to airway epithelia in vitro and in vivo
-
Walters RW, Duan D, Engelhardt JF, Welsh MJ (2000) Incorporation of adenoassociated virus in a calcium phosphate coprecipitate improves gene transfer to airway epithelia in vitro and in vivo. J Virol 74(1): 535-540.
-
(2000)
J Virol
, vol.74
, Issue.1
, pp. 535-540
-
-
Walters, R.W.1
Duan, D.2
Engelhardt, J.F.3
Welsh, M.J.4
-
10
-
-
73849108190
-
Cationic lipid formulations alter the in vivo tropism of AAV2/9 vector in lung
-
Fein DE, Limberis MP, Maloney SF, Heath JM, Wilson JM, et al. (2009) Cationic lipid formulations alter the in vivo tropism of AAV2/9 vector in lung. Mol Ther 17(12): 2078-2087.
-
(2009)
Mol Ther
, vol.17
, Issue.12
, pp. 2078-2087
-
-
Fein, D.E.1
Limberis, M.P.2
Maloney, S.F.3
Heath, J.M.4
Wilson, J.M.5
-
11
-
-
27844563357
-
PEG conjugation moderately protects adeno-associated viral vectors against antibody neutralization
-
Lee GK, Maheshri N, Kaspar B, Schaffer DV (2005) PEG conjugation moderately protects adeno-associated viral vectors against antibody neutralization. Biotechnol Bioeng 92(1): 24-34.
-
(2005)
Biotechnol Bioeng
, vol.92
, Issue.1
, pp. 24-34
-
-
Lee, G.K.1
Maheshri, N.2
Kaspar, B.3
Schaffer, D.V.4
-
12
-
-
42049117918
-
Coating of adeno-associated virus with reactive polymers can ablate virus tropism, enable retargeting and provide resistance to neutralising antisera
-
Carlisle RC, Benjamin R, Briggs SS, Sumner-Jones S, McIntosh J, et al. (2008) Coating of adeno-associated virus with reactive polymers can ablate virus tropism, enable retargeting and provide resistance to neutralising antisera. J Gene Med 10(4): 400-411.
-
(2008)
J Gene Med
, vol.10
, Issue.4
, pp. 400-411
-
-
Carlisle, R.C.1
Benjamin, R.2
Briggs, S.S.3
Sumner-Jones, S.4
McIntosh, J.5
-
13
-
-
44649137607
-
Polyinosinic acid enhances delivery of adenovirus vectors in vivo by preventing sequestration in liver macrophages
-
Haisma HJ, Kamps JA, Kamps GK, Plantinga JA, Rots MG, et al. (2008) Polyinosinic acid enhances delivery of adenovirus vectors in vivo by preventing sequestration in liver macrophages. J Gen Virol 89(Pt 5): 1097-1105.
-
(2008)
J Gen Virol
, vol.89
, Issue.PART 5
, pp. 1097-1105
-
-
Haisma, H.J.1
Kamps, J.A.2
Kamps, G.K.3
Plantinga, J.A.4
Rots, M.G.5
-
14
-
-
0031906147
-
Membrane-associated heparan sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions
-
Summerford C, Samulski RJ (1998) Membrane-associated heparan sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions. J Virol 72(2): 1438-1445.
-
(1998)
J Virol
, vol.72
, Issue.2
, pp. 1438-1445
-
-
Summerford, C.1
Samulski, R.J.2
-
15
-
-
0033998692
-
Infectious entry pathway of adenoassociated virus and adeno-associated virus vectors
-
Bartlett JS, Wilcher R, Samulski RJ (2000) Infectious entry pathway of adenoassociated virus and adeno-associated virus vectors. J Virol 74(6): 2777-2785.
-
(2000)
J Virol
, vol.74
, Issue.6
, pp. 2777-2785
-
-
Bartlett, J.S.1
Wilcher, R.2
Samulski, R.J.3
-
16
-
-
0038618725
-
Identification of amino acid residues in the capsid proteins of adeno-associated virus type 2 that contribute to heparan sulfate proteoglycan binding
-
Opie SR, Warrington KH, Jr., Agbandje-McKenna M, Zolotukhin S, Muzyczka N (2003) Identification of amino acid residues in the capsid proteins of adeno-associated virus type 2 that contribute to heparan sulfate proteoglycan binding. J Virol 77(12): 6995-7006.
-
(2003)
J Virol
, vol.77
, Issue.12
, pp. 6995-7006
-
-
Opie, S.R.1
Warrington Jr., K.H.2
Agbandje-McKenna, M.3
Zolotukhin, S.4
Muzyczka, N.5
-
17
-
-
33745776920
-
Heparan sulfate proteoglycan binding properties of adeno-associated virus retargeting mutants and consequences for their in vivo tropism
-
Perabo L, Goldnau D, White K, Endell J, Boucas J, et al. (2006) Heparan sulfate proteoglycan binding properties of adeno-associated virus retargeting mutants and consequences for their in vivo tropism. J Virol 80(14): 7265-7269.
-
(2006)
J Virol
, vol.80
, Issue.14
, pp. 7265-7269
-
-
Perabo, L.1
Goldnau, D.2
White, K.3
Endell, J.4
Boucas, J.5
-
18
-
-
0029981092
-
Evidence for the role of proteoglycans in cation-mediated gene transfer
-
Mislick KA, Baldeschwieler JD (1996) Evidence for the role of proteoglycans in cation-mediated gene transfer. Proc Natl Acad Sci U S A 93(22): 12349-12354.
-
(1996)
Proc Natl Acad Sci U S A
, vol.93
, Issue.22
, pp. 12349-12354
-
-
Mislick, K.A.1
Baldeschwieler, J.D.2
-
19
-
-
0035138205
-
Intracellular trafficking of adeno-associated virus vectors: Routing to the late endosomal compartment and proteasome degradation
-
Douar AM, Poulard K, Stockholm D, Danos O (2001) Intracellular trafficking of adeno-associated virus vectors: routing to the late endosomal compartment and proteasome degradation. J Virol 75(4): 1824-1833.
-
(2001)
J Virol
, vol.75
, Issue.4
, pp. 1824-1833
-
-
Douar, A.M.1
Poulard, K.2
Stockholm, D.3
Danos, O.4
-
20
-
-
2642642141
-
Production of high-titer recombinant adenoassociated virus vectors in the absence of helper adenovirus
-
Xiao X, Li J, Samulski RJ (1998) Production of high-titer recombinant adenoassociated virus vectors in the absence of helper adenovirus. J Virol 72(3): 2224-2232.
-
(1998)
J Virol
, vol.72
, Issue.3
, pp. 2224-2232
-
-
Xiao, X.1
Li, J.2
Samulski, R.J.3
-
21
-
-
0035861219
-
MUSEAP, a novel reporter gene for the study of long-term gene expression in immunocompetent mice
-
Wang M, Orsini C, Casanova D, Millan JL, Mahfoudi A, et al. (2001) MUSEAP, a novel reporter gene for the study of long-term gene expression in immunocompetent mice. Gene 279(1): 99-108.
-
(2001)
Gene
, vol.279
, Issue.1
, pp. 99-108
-
-
Wang, M.1
Orsini, C.2
Casanova, D.3
Millan, J.L.4
Mahfoudi, A.5
-
22
-
-
33846300685
-
Design of tissue-specific regulatory cassettes for high-level rAAV-mediated expression in skeletal and cardiac muscle
-
Salva MZ, Himeda CL, Tai PW, Nishiuchi E, Gregorevic P, et al. (2007) Design of tissue-specific regulatory cassettes for high-level rAAV-mediated expression in skeletal and cardiac muscle. Mol Ther 15(2): 320-329.
-
(2007)
Mol Ther
, vol.15
, Issue.2
, pp. 320-329
-
-
Salva, M.Z.1
Himeda, C.L.2
Tai, P.W.3
Nishiuchi, E.4
Gregorevic, P.5
-
23
-
-
0026586140
-
Expression of human alpha 1-antitrypsin in dogs after autologous transplantation of retroviral transduced hepatocytes
-
Kay MA, Baley P, Rothenberg S, Leland F, Fleming L, et al. (1992) Expression of human alpha 1-antitrypsin in dogs after autologous transplantation of retroviral transduced hepatocytes. Proc Natl Acad Sci U S A 89(1): 89-93.
-
(1992)
Proc Natl Acad Sci U S A
, vol.89
, Issue.1
, pp. 89-93
-
-
Kay, M.A.1
Baley, P.2
Rothenberg, S.3
Leland, F.4
Fleming, L.5
-
24
-
-
9244230548
-
The enhancer domain of the human cytomegalovirus major immediate-early promoter determines cell type-specific expression in transgenic mice
-
Baskar JF, Smith PP, Nilaver G, Jupp RA, Hoffmann S, et al. (1996) The enhancer domain of the human cytomegalovirus major immediate-early promoter determines cell type-specific expression in transgenic mice. J Virol 70(5): 3207-3214.
-
(1996)
J Virol
, vol.70
, Issue.5
, pp. 3207-3214
-
-
Baskar, J.F.1
Smith, P.P.2
Nilaver, G.3
Jupp, R.A.4
Hoffmann, S.5
-
25
-
-
44049085243
-
Toward exascale production of recombinant adeno-associated virus for gene transfer applications
-
Cecchini S, Negrete A, Kotin RM (2008) Toward exascale production of recombinant adeno-associated virus for gene transfer applications. Gene Ther 15(11): 823-830.
-
(2008)
Gene Ther
, vol.15
, Issue.11
, pp. 823-830
-
-
Cecchini, S.1
Negrete, A.2
Kotin, R.M.3
-
26
-
-
0001441956
-
Antineoplastic activity of poly(L-lysine) with some ascites tumor cells
-
Arnold LJ, Jr., Dagan A, Gutheil J, Kaplan NO (1979) Antineoplastic activity of poly(L-lysine) with some ascites tumor cells. Proc Natl Acad Sci U S A 76(7): 3246-3250.
-
(1979)
Proc Natl Acad Sci U S A
, vol.76
, Issue.7
, pp. 3246-3250
-
-
Arnold Jr., L.J.1
Dagan, A.2
Gutheil, J.3
Kaplan, N.O.4
-
27
-
-
0035916312
-
The eosinophil peroxidase-hydrogen peroxide-bromide system of human eosinophils generates 5-bromouracil, a mutagenic thymine analogue
-
Henderson JP, Byun J, Mueller DM, Heinecke JW (2001) The eosinophil peroxidase-hydrogen peroxide-bromide system of human eosinophils generates 5-bromouracil, a mutagenic thymine analogue. Biochemistry 40(7): 2052-2059.
-
(2001)
Biochemistry
, vol.40
, Issue.7
, pp. 2052-2059
-
-
Henderson, J.P.1
Byun, J.2
Mueller, D.M.3
Heinecke, J.W.4
-
28
-
-
0034860703
-
Protamine sulfate enhances the transduction efficiency of recombinant adeno-associated virus-mediated gene delivery
-
Yang YW, Hsieh YC (2001) Protamine sulfate enhances the transduction efficiency of recombinant adeno-associated virus-mediated gene delivery. Pharm Res 18(7): 922-927.
-
(2001)
Pharm Res
, vol.18
, Issue.7
, pp. 922-927
-
-
Yang, Y.W.1
Hsieh, Y.C.2
-
29
-
-
0032855208
-
Efficient infection of mature skeletal muscle with herpes simplex virus vectors by using dextran sulfate as a coreceptor
-
Yeung SN, Bockhold K, Tufaro F (1999) Efficient infection of mature skeletal muscle with herpes simplex virus vectors by using dextran sulfate as a coreceptor. Gene Ther 6(9): 1536-1544.
-
(1999)
Gene Ther
, vol.6
, Issue.9
, pp. 1536-1544
-
-
Yeung, S.N.1
Bockhold, K.2
Tufaro, F.3
|