Intrathecal enzyme replacement therapy to treat spinal cord compression in mucopolysaccharidosis: Overview and rationale

Journal of Pediatric Rehabilitation Medicine

Volumn 3, Issue 1, 2010, Pages 7-11

  Chen, Agnes ^a   Dickson, Patricia ^a  

^a HARBOR UCLA MEDICAL CENTER   (United States)

Author keywords

Mucopolysaccharidosis; Spinal cord

Indexed keywords

LARONIDASE; PEPTIDE HYDROLASE; RECOMBINANT ENZYME; SULFAMIDASE; TRIPEPTIDYL PEPTIDASE I; UNCLASSIFIED DRUG;

CEREBROSPINAL FLUID; CERVICAL MYELOPATHY; CLINICAL TRIAL; CRANIECTOMY; DECOMPRESSION SURGERY; ENZYME REPLACEMENT; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; HURLER SYNDROME; IMMUNE RESPONSE; LAMINECTOMY; MUCOPOLYSACCHARIDOSIS; NEURONAL CEROID LIPOFUSCINOSIS; NONHUMAN; NOTE; PRIORITY JOURNAL; SANFILIPPO SYNDROME; SPINAL CORD COMPRESSION;

EID: 77953444836     PISSN: 18745393     EISSN: 18758894     Source Type: Journal    
DOI: 10.3233/PRM-2010-0107     Document Type: Note

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