Inefficient dystrophin expression after cord blood transplantation in duchenne muscular dystrophy

Muscle and Nerve

Volumn 41, Issue 6, 2010, Pages 746-750

  Kang, Peter B ^a,b   Lidov, Hart G W ^a   White, Alexander J ^a   Mitchell, Matthew ^a   Balasubramanian, Anuradha ^a   Estrella, Elicia ^a   Bennett, Richard R ^a   Darras, Basil T ^b   Shapiro, Frederic D ^a   Bambach, Barbara J ^c   Kurtzberg, Joanne ^d   Gussoni, Emanuela ^a   Kunkel, Louis M ^a  

^a BOSTON CHILDREN S HOSPITAL   (United States)

^b HARVARD MEDICAL SCHOOL   (United States)

^c ROSWELL PARK CANCER INSTITUTE   (United States)

^d DUKE UNIVERSITY MEDICAL CENTER   (United States)

Author keywords

Chronic granulomatous disease; Duchenne muscular dystrophy; Dystrophin; Stem cell therapy; Umbilical cord blood transplantation

Indexed keywords

ALEMTUZUMAB; BUSULFAN; CYCLOPHOSPHAMIDE; DNA; DYSTROPHIN; FLUDARABINE; THYMOCYTE ANTIBODY;

ALLOGENEIC STEM CELL TRANSPLANTATION; ARTICLE; BLOOD DONOR; CASE REPORT; CELL CULTURE; CHILD; CHROMOSOME DELETION X; CHRONIC GRANULOMATOUS DISEASE; CORD BLOOD STEM CELL TRANSPLANTATION; DUCHENNE MUSCULAR DYSTROPHY; ENGRAFTMENT; GRAFT REJECTION; HUMAN; HUMAN CELL; HUMAN TISSUE; IMMUNOHISTOCHEMISTRY; MALE; MUSCLE BIOPSY; MUSCLE TISSUE; MYOBLAST; PRESCHOOL CHILD; PRIORITY JOURNAL; PROTEIN EXPRESSION; SKELETAL MUSCLE;

ANTIBODIES, MONOCLONAL; ANTIBODIES, NEOPLASM; CHILD; CHROMOSOME MAPPING; CHROMOSOMES, HUMAN, X; CYCLOPHOSPHAMIDE; DYSTROPHIN; FOLLOW-UP STUDIES; GENE DELETION; GENE EXPRESSION REGULATION; GRANULOMATOUS DISEASE, CHRONIC; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMANS; MALE; MUSCULAR DYSTROPHY, DUCHENNE; REOPERATION; TRANSPLANTATION, HOMOLOGOUS; TREATMENT OUTCOME; VIDARABINE;

EID: 77953116226     PISSN: 0148639X     EISSN: 10974598     Source Type: Journal    
DOI: 10.1002/mus.21702     Document Type: Article

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