Alternative pathway or diversion therapy for urea cycle disorders now and in the future

Molecular Genetics and Metabolism

Volumn 100, Issue 3, 2010, Pages 219-220

  Cederbaum, Stephen ^a   LeMons, Cynthia ^b   Batshaw, Mark L ^c  

^a UNIVERSITY OF CALIFORNIA   (United States)

^b National Urea Cycle Disorders Foundation   (United States)

^c GEORGE WASHINGTON UNIVERSITY SCHOOL OF MEDICINE AND HEALTH SCIENCES   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

4 PHENYLBUTYRIC ACID; AMMONIA; AMMONUL; BENZOIC ACID; GLYCEROL TRIBENZOATE; GLYCEROL TRIPHENYLACETATE; GLYCEROTRIPHENYLBUTYRATE; PHENYLACETATE SODIUM; PHENYLACETIC ACID; UNCLASSIFIED DRUG;

ARTICLE; CLINICAL TRIAL; DISEASE ASSOCIATION; DRUG APPROVAL; DRUG COST; DRUG EFFICACY; DRUG MARKETING; DRUG TOLERABILITY; FOOD AND DRUG ADMINISTRATION; HEALTH INSURANCE; HUMAN; HYPERAMMONEMIA; LICENCE; NONHUMAN; PRIORITY JOURNAL; UREA CYCLE DISORDER;

EID: 77953023545     PISSN: 10967192     EISSN: 10967206     Source Type: Journal    
DOI: 10.1016/j.ymgme.2010.04.008     Document Type: Note

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