Bone marrow transplantation for inherited bone marrow failure syndromes

Pediatric Clinics of North America

Volumn 57, Issue 1, 2010, Pages 147-170

  Mehta, Parinda ^a   Locatelli, Franco ^b,c   Stary, Jan ^d   Smith, Franklin O ^a  

^a CINCINNATI CHILDREN'S HOSPITAL MEDICAL CENTER   (United States)

^b UNIVERSITY OF PAVIA   (Italy)

^c FONDAZIONE IRCCS POLICLINICO SAN MATTEO   (Italy)

^d UNIVERSITY HOSPITAL MOTOL   (Czech Republic)

Author keywords

Bone marrow transplantation; Diagnostic tests; Gene mutation; Inherited bone marrow failure syndromes

Indexed keywords

ALKYLATING AGENT; ANDROGEN; BUSULFAN; CORTICOSTEROID; CYCLOPHOSPHAMIDE; CYCLOSPORIN; ERYTHROPOIETIN; FLUDARABINE; GRANULOCYTE COLONY STIMULATING FACTOR; INTERLEUKIN 11; INTERLEUKIN 3; MELPHALAN; METHOTREXATE; STEROID; TACROLIMUS; THYMOCYTE ANTIBODY; TREOSULFAN;

ACUTE GRAFT VERSUS HOST DISEASE; ACUTE GRANULOCYTIC LEUKEMIA; ALLOGENEIC HEMATOPOIETIC STEM CELL TRANSPLANTATION; BLACKFAN DIAMOND ANEMIA; BLOOD TRANSFUSION; BONE MARROW DEPRESSION; BONE MARROW TRANSPLANTATION; CANCER RADIOTHERAPY; CANCER SUSCEPTIBILITY; CHRONIC GRAFT VERSUS HOST DISEASE; CLINICAL FEATURE; CLINICAL TRIAL; CORD BLOOD STEM CELL TRANSPLANTATION; DIAGNOSTIC VALUE; DRUG RESPONSE; DRUG SENSITIVITY; DYSKERATOSIS CONGENITA; ERYTHROCYTE TRANSFUSION; FANCONI ANEMIA; GENE MUTATION; GRAFT FAILURE; GRAFT REJECTION; GRAFT VERSUS HOST REACTION; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; LIVER TOXICITY; LOW DRUG DOSE; MYELODYSPLASTIC SYNDROME; PATIENT SAFETY; REVIEW; SENSITIVITY AND SPECIFICITY; SHWACHMAN SYNDROME; THROMBOCYTOPENIA; UNSPECIFIED SIDE EFFECT; VIRILIZATION; WHOLE BODY RADIATION;

BONE MARROW DISEASES; BONE MARROW TRANSPLANTATION; FANCONI ANEMIA; GENETIC PREDISPOSITION TO DISEASE; HUMANS; SYNDROME; TREATMENT OUTCOME;

EID: 77951029213     PISSN: 00313955     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.pcl.2010.01.002     Document Type: Review

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