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Volumn 16, Issue 3, 2010, Pages 241-
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Rare opportunities appear on the horizon to treat rare diseases
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Author keywords
[No Author keywords available]
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Indexed keywords
ENZYME REPLACEMENT;
FOOD AND DRUG ADMINISTRATION;
MARKETING;
MEDICAL RESEARCH;
NOTE;
PRIORITY JOURNAL;
RARE DISEASE;
DRUG INDUSTRY;
HUMANS;
ORPHAN DRUG PRODUCTION;
RARE DISEASES;
UNITED STATES;
UNITED STATES FOOD AND DRUG ADMINISTRATION;
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EID: 77749239768
PISSN: 10788956
EISSN: 1546170X
Source Type: Journal
DOI: 10.1038/nm0310-241 Document Type: Note |
Times cited : (7)
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References (0)
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