Correction of mutant Fanconi anemia gene by homologous recombination in human hematopoietic cells using adeno-associated virus vector

Journal of Gene Medicine

Volumn 11, Issue 11, 2009, Pages 1012-1019

  Paiboonsukwong, Kittiphong ^a   Ohbayashi, Fumi ^a   Shiiba, Haruka ^a   Aizawa, Emi ^a   Yamashita, Takayuki ^b   Mitani, Kohnosuke ^a  

^a SAITAMA MEDICAL UNIVERSITY   (Japan)

^b GUNMA UNIVERSITY   (Japan)

Author keywords

Adeno associated virus; Fanconi anemia; Gene repair; Hematopoietic; Homologous recombination

Indexed keywords

FANCONI ANEMIA GROUP A PROTEIN; HYPOXANTHINE PHOSPHORIBOSYLTRANSFERASE; PARVOVIRUS VECTOR;

ARTICLE; CONTROLLED STUDY; DAUDI CELL; DRUG MECHANISM; FANCONI ANEMIA; GENE EXPRESSION; GENE LOCUS; GENE MUTATION; GENE TARGETING; GENOTYPE; HEMATOPOIETIC CELL; HOMOLOGOUS RECOMBINATION; HUMAN; HUMAN CELL; MUTANT; PHENOTYPE; PRIORITY JOURNAL; VIRAL GENE DELIVERY SYSTEM; VIRAL GENE THERAPY;

CELLS, CULTURED; DEPENDOVIRUS; FANCONI ANEMIA COMPLEMENTATION GROUP A PROTEIN; GENE TARGETING; GENETIC VECTORS; HUMANS; HYPOXANTHINE PHOSPHORIBOSYLTRANSFERASE; MODELS, GENETIC; MUTATION; RECOMBINATION, GENETIC; TRANSDUCTION, GENETIC;

ADENO-ASSOCIATED VIRUS;

EID: 72949084251     PISSN: 1099498X     EISSN: 15212254     Source Type: Journal    
DOI: 10.1002/jgm.1382     Document Type: Article

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