Multidisciplinary management of Hunter syndrome

Pediatrics

Volumn 124, Issue 6, 2009, Pages

  Muenzer, Joseph ^a   Beck, M ^b   Eng, C M ^c   Escolar, M L ^a   Giugliani, R ^d   Guffon, N H ^e   Harmatz, P ^f   Kamin, W ^b   Kampmann, C ^b   Koseoglu, S T ^f   Link, B ^g   Martin, R A ^h,p   Molter, D W ⁱ   Rojas, M V Muñoz ^d   Ogilvie, J W ^j   Parini, R ^k   Ramaswami, U ^l   Scarpa, L M ^m   Schwartz, I V ^d   Wood, R E ⁿ   Wraith, E ^o   more..

^a UNIVERSITY OF NORTH CAROLINA SCHOOL OF MEDICINE   (United States)

^b JOHANNES GUTENBERG UNIVERSITY   (Germany)

^c BAYLOR COLLEGE OF MEDICINE   (United States)

^d HOSPITAL DE CLÍNICAS DE PORTO ALEGRE   (Brazil)

^e EDOUARD HERRIOT HOSPITAL   (France)

^f CHILDREN S HOSPITAL OAKLAND   (United States)

^g UNIVERSITY MEDICAL CENTER MAINZ   (Germany)

^h SAINT LOUIS UNIVERSITY SCHOOL OF MEDICINE   (United States)

ⁱ WASHINGTON UNIVERSITY   (United States)

^j UNIVERSITY OF UTAH SCHOOL OF MEDICINE   (United States)

^k SAN GERARDO HOSPITAL   (Italy)

^l ADDENBROOKE S HOSPITAL   (United Kingdom)

^m UNIVERSITY OF PADOVA   (Italy)

ⁿ CINCINNATI CHILDREN'S HOSPITAL MEDICAL CENTER   (United States)

^o ST MARY S HOSPITAL   (United Kingdom)

^p SHIRE   (United States)

more..

Author keywords

Enzyme replacement therapy; Hunter syndrome; Lysosomal storage diseases; Mucopolysaccharidosis II

Indexed keywords

ADRENALIN; ANTICONVULSIVE AGENT; ANTIHISTAMINIC AGENT; BETA ADRENERGIC RECEPTOR STIMULATING AGENT; CORTICOSTEROID; GLYCOSAMINOGLYCAN; IDURONATE 2 SULFATASE; PLACEBO;

AIRWAY OBSTRUCTION; ANAPHYLAXIS; AUDIOLOGY; BEHAVIOR DISORDER; BRONCHOSCOPY; CARPAL TUNNEL SYNDROME; CLINICAL ASSESSMENT; CLINICAL FEATURE; CLINICAL TRIAL; COMMUNICATING HYDROCEPHALUS; CONTROLLED CLINICAL TRIAL; DECOMPRESSION SURGERY; DIAGNOSTIC IMAGING; DRUG DOSE REDUCTION; DRUG ERUPTION; DRUG FEVER; DRUG INDUCED HEADACHE; DRUG TOLERABILITY; DRUG WITHDRAWAL; DYSPHAGIA; ECHOCARDIOGRAPHY; ENZYME ACTIVITY; ENZYME REPLACEMENT; ERYTHEMA; FIBROBLAST; FLUSHING; GENOTYPE; HEARING AID; HEARING LOSS; HEART DISEASE; HUMAN; HUNTER SYNDROME; HURLER SYNDROME; INTUBATION; LUNG FUNCTION TEST; LYSOSOME; MULTIPLE ORGAN FAILURE; MYRINGOTOMY; NERVE CELL DIFFERENTIATION; NERVOUS SYSTEM INJURY; NUCLEAR MAGNETIC RESONANCE IMAGING; OPTIC NERVE LESION; ORTHOPEDIC SURGERY; PALLIATIVE THERAPY; PHENOTYPE; PHYSICAL EXAMINATION; PHYSIOTHERAPY; PLASMA TRANSFUSION; POSITIVE END EXPIRATORY PRESSURE; PRIORITY JOURNAL; RANDOMIZED CONTROLLED TRIAL; REVIEW; SEIZURE; SHORT STATURE; SIDE EFFECT; SKELETON MALFORMATION; SPINAL CORD COMPRESSION; STEM CELL TRANSPLANTATION; TERMINAL CARE; TOOTH MALFORMATION; TRACHEOTOMY; UPPER RESPIRATORY TRACT OBSTRUCTION; URTICARIA; VALVULAR HEART DISEASE; X CHROMOSOME LINKED DISORDER;

ADOLESCENT; ADULT; CHILD; CHILD, PRESCHOOL; COMBINED MODALITY THERAPY; COOPERATIVE BEHAVIOR; ENZYME REPLACEMENT THERAPY; GENOTYPE; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMANS; IDURONATE SULFATASE; INFANT; INFANT, NEWBORN; INFUSIONS, INTRAVENOUS; INTERDISCIPLINARY COMMUNICATION; MALE; MUCOPOLYSACCHARIDOSIS II; PATIENT CARE TEAM; PHENOTYPE; RANDOMIZED CONTROLLED TRIALS AS TOPIC; RECOMBINANT PROTEINS; YOUNG ADULT;

EID: 71949110878     PISSN: 00314005     EISSN: 10984275     Source Type: Journal    
DOI: 10.1542/peds.2008-0999     Document Type: Review

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