Patient Registries and Trial Readiness in Myotonic Dystrophy - TREAT-NMD/Marigold International Workshop Report

Neuromuscular Disorders

Volumn 19, Issue 12, 2009, Pages 860-866

  Thompson, Rachel ^a   Schoser, Benedikt ^b   Monckton, Darren G ^c   Blonsky, Karla ^d   Lochmüller, Hanns ^a  

^a NEWCASTLE UNIVERSITY   (United Kingdom)

^b LUDWIG MAXIMILIANS UNIVERSITY   (Germany)

^c UNIVERSITY OF GLASGOW   (United Kingdom)

^d Marigold Foundation   (Canada)

Author keywords

[No Author keywords available]

Indexed keywords

ALPHA TOCOPHEROL; AMITRIPTYLINE; ANTISENSE OLIGONUCLEOTIDE; GROWTH HORMONE; HUMAN GROWTH HORMONE; IMIPRAMINE; PLACEBO; PRASTERONE SULFATE; RECOMBINANT SOMATOMEDIN C; SELENIUM; TESTOSTERONE ENANTATE;

ANTISENSE THERAPY; ARTICLE; ASSISTED VENTILATION; CLINICAL RESEARCH; CLINICAL TRIAL; DISEASE REGISTRY; DRUG DOSE COMPARISON; DRUG DOSE ESCALATION; DUCHENNE MUSCULAR DYSTROPHY; GENETIC ANALYSIS; HEART ARRHYTHMIA; HUMAN; KINESIOTHERAPY; LYSOSOME STORAGE DISEASE; MUSCLE STRENGTH; MUSCLE WEAKNESS; MYOTONIC DYSTROPHY; NONHUMAN; OUTCOME ASSESSMENT; PATIENT PARTICIPATION; PRIORITY JOURNAL;

CLINICAL TRIALS AS TOPIC; DATABASES AS TOPIC; HUMANS; INTERNATIONAL COOPERATION; MYOTONIC DYSTROPHY; REGISTRIES; SEVERITY OF ILLNESS INDEX; TREATMENT OUTCOME;

EID: 70449528337     PISSN: 09608966     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.nmd.2009.08.009     Document Type: Article

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