Oral Cholic Acid for Hereditary Defects of Primary Bile Acid Synthesis: A Safe and Effective Long-term Therapy

Gastroenterology

Volumn 137, Issue 4, 2009, Pages

  Gonzales, Emmanuel ^a,b,c   Gerhardt, Marie F ^d   Fabre, Monique ^a,b   Setchell, Kenneth D R ^e   Davit Spraul, Anne ^a   Vincent, Isabelle ^a   Heubi, James E ^e   Bernard, Olivier ^a,b   Jacquemin, Emmanuel ^a,b,c  

^a BICÊTRE HOSPITAL   (France)

^b UNIVERSITÉ PARIS SACLAY   (France)

^c INSERM   (France)

^d SAINT JOSEPH HOSPITAL   (France)

^e CINCINNATI CHILDREN'S HOSPITAL MEDICAL CENTER   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

3(OR 17)BETA HYDROXYSTEROID DEHYDROGENASE; CHOLIC ACID; STEROID 5BETA REDUCTASE; 3 BETA HYDROXY DELTA 5 C(27) STEROID DEHYDROGENASE; 3 BETA-HYDROXY-DELTA 5-C(27)-STEROID DEHYDROGENASE; BILE ACID; CHOLAGOGUE; CHOLESTENONE 5 BETA REDUCTASE; CHOLESTENONE 5 BETA-REDUCTASE; OXIDOREDUCTASE;

3(OR 17)BETA HYDROXYSTEROID DEHYDROGENASE DEFICIENCY; ADOLESCENT; ALANINE AMINOTRANSFERASE BLOOD LEVEL; ARTICLE; BILE ACID BLOOD LEVEL; BILE ACID SYNTHESIS; BILE DUCT DISEASE; BILIARY EXCRETION; CHILD; CLINICAL ARTICLE; CLINICAL TRIAL; DIARRHEA; DRUG DOSE REDUCTION; DRUG EFFICACY; DRUG SAFETY; DRUG TOLERABILITY; ECHOGRAPHY; EMBRYOTOXICITY; ENZYME DEFICIENCY; FEMALE; FOLLOW UP; GENE SEQUENCE; HUMAN; HUMAN TISSUE; INFANT; LABORATORY TEST; LIVER BIOPSY; LONG TERM CARE; MALE; MASS SPECTROMETRY; PHYSICAL EXAMINATION; PREGNANCY; PRESCHOOL CHILD; PRIORITY JOURNAL; PROSPECTIVE STUDY; PRURITUS; SCHOOL CHILD; SIDE EFFECT; STEROID 5BETA REDUCTASE DEFICIENCY; TREATMENT OUTCOME; UNSPECIFIED SIDE EFFECT; URINALYSIS; URINARY EXCRETION; BIOPSY; DRUG ADMINISTRATION; DRUG EFFECT; ENZYMOLOGY; FAST ATOM BOMBARDMENT MASS SPECTROMETRY; INBORN ERROR OF METABOLISM; LIVER; MASS FRAGMENTOGRAPHY; METABOLISM; ORAL DRUG ADMINISTRATION; PATHOLOGY; TIME;

3-HYDROXYSTEROID DEHYDROGENASES; ADMINISTRATION, ORAL; ADOLESCENT; BILE ACIDS AND SALTS; BIOPSY; CHILD; CHILD, PRESCHOOL; CHOLAGOGUES AND CHOLERETICS; CHOLIC ACID; DRUG ADMINISTRATION SCHEDULE; FEMALE; GAS CHROMATOGRAPHY-MASS SPECTROMETRY; HUMANS; INFANT; LIVER; MALE; METABOLISM, INBORN ERRORS; OXIDOREDUCTASES; PROSPECTIVE STUDIES; SPECTROMETRY, MASS, FAST ATOM BOMBARDMENT; TIME FACTORS; TREATMENT OUTCOME;

EID: 70349414388     PISSN: 00165085     EISSN: None     Source Type: Journal    
DOI: 10.1053/j.gastro.2009.07.043     Document Type: Article

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