Pathogenesis of leukodystrophy for Krabbe disease: Molecular mechanism and clinical treatment

Brain and Development

Volumn 31, Issue 7, 2009, Pages 485-487

  Sakai, Norio ^a  

^a OSAKA UNIVERSITY GRADUATE SCHOOL OF MEDICINE   (Japan)

Author keywords

Globoid cell leukodystrophy; Hematopoietic stem cell transplantation; Krabbe disease

Indexed keywords

GALACTOSYLCERAMIDASE; SPHINGOLIPID ACTIVATOR PROTEIN;

ADRENOLEUKODYSTROPHY; CORD BLOOD STEM CELL TRANSPLANTATION; DEMYELINATION; DISEASE CLASSIFICATION; ENZYME REPLACEMENT; GLOBOID CELL LEUKODYSTROPHY; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; METACHROMATIC LEUKODYSTROPHY; MOLECULAR CLONING; MUTATIONAL ANALYSIS; NERVOUS SYSTEM INFLAMMATION; NEUROPATHOLOGY; NONHUMAN; PATHOGENESIS; REVIEW;

GALACTOSYLCERAMIDASE; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMANS; LEUKODYSTROPHY, GLOBOID CELL; MUTATION;

EID: 67649432567     PISSN: 03877604     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.braindev.2009.03.001     Document Type: Review

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