Outcome measures in Duchenne muscular dystrophy: Are we ready for the new therapeutic era?

Neuromuscular Disorders

Volumn 19, Issue 6, 2009, Pages 447-

  Merkies, Ingemar S J ^a,b   Faber, Catharina G ^a  

^a MAASTRICHT UNIVERSITY MEDICAL CENTER   (Netherlands)

^b Department of Orthopaedic Surgery   (Netherlands)

Author keywords

[No Author keywords available]

Indexed keywords

DUCHENNE MUSCULAR DYSTROPHY; HUMAN; LETTER; MEDICAL ASSESSMENT; OUTCOME ASSESSMENT; PATIENT CARE; PRIORITY JOURNAL; RASCH ANALYSIS; RATING SCALE; RELIABILITY; SCORING SYSTEM; VALIDITY; WALKING;

HUMANS; MUSCULAR DYSTROPHY, DUCHENNE; SEVERITY OF ILLNESS INDEX; TREATMENT OUTCOME;

EID: 67349101615     PISSN: 09608966     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.nmd.2009.04.005     Document Type: Letter

References (7)

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2. Merbitz C., Morris J., and Grip J.C. Ordinal scales and foundations of misinference. Arch Phys Med Rehabil 70 (1989) 308-312
3. Wright B.D., and Linacre J.M. Observations are always ordinal; measurements, however, must be interval. Arch Phys Med Rehabil 70 (1989) 857-860
4. Jaeschke R., Singer J., and Guyatt G.H. Ascertaining the minimal clinically important difference. Control Clin Trials 10 (1989) 407-415
5. Sloan J., Symonds T., Vargas-Chanes D., and Fridley B. Practical guidelines for assessing the clinical significance of health-related quality of life changes within clinical trials. Drug Inform J 37 (2003) 23-31
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7. Vandervelde L., Van den Bergh P.Y., Goemans N., and Thonnard J.L. ACTIVLIM: a Rasch-built measure of activity limitations in children and adults with neuromuscular disorders. Neuromuscul Disord 17 (2007) 459-469