Kinetin in familial dysautonomia carriers: Implications for a new therapeutic strategy targeting mRNA splicing

Pediatric Research

Volumn 65, Issue 3, 2009, Pages 341-346

  Simson, Gabrielle Gold Von ^a,d   Goldberg, Judith D ^a   Rolnitzky, Linda M ^a   Mull, James ^b,c   Leyne, Maire ^b,c   Voustianiouk, Andrei ^a   Slaugenhaupt, Susan A ^b,c   Axelrod, Felicia B ^a  

^a NEW YORK UNIVERSITY SCHOOL OF MEDICINE   (United States)

^b MASSACHUSETTS GENERAL HOSPITAL   (United States)

^c HARVARD MEDICAL SCHOOL   (United States)

^d NEW YORK UNIVERSITY MEDICAL CENTER   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

CYTOKINE; I KAPPA B KINASE ASSOCIATED PROTEIN; KINETIN; MESSENGER RNA; UNCLASSIFIED DRUG;

ADULT; AREA UNDER THE CURVE; ARTICLE; CELL LEVEL; CLINICAL ARTICLE; CONTROLLED STUDY; DIARRHEA; DOSE RESPONSE; DRUG BLOOD LEVEL; DRUG ERUPTION; DRUG SAFETY; DYSAUTONOMIA; FEMALE; GENE MUTATION; HEADACHE; HUMAN; IN VIVO STUDY; MALE; NAUSEA; PRIORITY JOURNAL; RNA SPLICING; TINNITUS;

ADULT; ALTERNATIVE SPLICING; CARRIER PROTEINS; DOSE-RESPONSE RELATIONSHIP, DRUG; DYSAUTONOMIA, FAMILIAL; FEMALE; GENE EXPRESSION REGULATION; HETEROZYGOTE; HUMANS; KINETIN; MALE; MUTATION; RNA, MESSENGER; STATISTICS, NONPARAMETRIC;

EID: 61949408123     PISSN: 00313998     EISSN: 15300447     Source Type: Journal    
DOI: 10.1203/PDR.0b013e318194fd52     Document Type: Article

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