Murine muscle cell models for Pompe disease and their use in studying therapeutic approaches

Molecular Genetics and Metabolism

Volumn 96, Issue 4, 2009, Pages 208-217

  Takikita, Shoichi ^a   Myerowitz, Rachel ^a,b   Zaal, Kristien ^a   Raben, Nina ^a   Plotz, Paul H ^a  

^a NATIONAL INSTITUTE OF ARTHRITIS AND MUSCULOSKELETAL AND SKIN DISEASES   (United States)

^b ST MARY'S COLLEGE OF MARYLAND   (United States)

Author keywords

Autophagy; Lysosomes; Myotubes; Pompe disease

Indexed keywords

ALPHA GLUCOSIDASE; CYCLIN DEPENDENT KINASE 4; GLYCOGEN; RECOMBINANT HUMAN ALPHA GLUCOSIDASE; SMALL INTERFERING RNA; UNCLASSIFIED DRUG;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; ATG7 GENE; AUTOPHAGY; CARDIOMYOPATHY; CELL PROLIFERATION; CONTROLLED STUDY; DISEASE MODEL; ENZYME REPLACEMENT; GENE; GENOTYPE; GLYCOGEN STORAGE DISEASE TYPE 2; IN VITRO STUDY; LYSOSOME; MOUSE; MUSCLE CELL; MYOPATHY; MYOTUBE; NEWBORN; NONHUMAN; PRIORITY JOURNAL; UBIQUITINATION;

ALPHA-GLUCOSIDASES; ANIMALS; AUTOPHAGY; CATHEPSIN B; CATHEPSIN D; CELLS, CULTURED; CYCLIN-DEPENDENT KINASE 4; DISEASE MODELS, ANIMAL; ENDOCYTOSIS; GLYCOGEN STORAGE DISEASE TYPE II; HUMANS; HYDROGEN-ION CONCENTRATION; LYSOSOMES; MICE; MICROTUBULE-ASSOCIATED PROTEINS; MUSCLE CELLS; MUSCLE FIBERS, SKELETAL; MYOBLASTS; RNA, SMALL INTERFERING; TRANSDUCTION, GENETIC;

MURINAE; MUS;

EID: 61849085267     PISSN: 10967192     EISSN: 10967206     Source Type: Journal    
DOI: 10.1016/j.ymgme.2008.12.012     Document Type: Article

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