Recombinant adeno-associated virus-mediated gene delivery of long chain acyl coenzyme A dehydrogenase (LCAD) into LCAD-deficient mice

Journal of Gene Medicine

Volumn 10, Issue 10, 2008, Pages 1113-1123

  Beattie, Stuart G ^a   Goetzman, Eric ^b   Tang, Qiuishi ^a   Conlon, Thomas ^c   Campbell Thompson, Martha ^c   Matern, Dietrich ^d   Vockley, Jerry ^b   Flotte, Terence R ^a  

^a UNIVERSITY OF MASSACHUSETTS MEDICAL SCHOOL   (United States)

^b UNIVERSITY OF PITTSBURGH SCHOOL OF MEDICINE   (United States)

^c UNIVERSITY OF FLORIDA   (United States)

^d Mayo Clinic College of Medicine   (United States)

Author keywords

Adeno associated virus; Fatty acid oxidation; Gene therapy; LCAD; Liver; Mitochondria; Vector; VLCAD

Indexed keywords

ELECTRON TRANSFERRING FLAVOPROTEIN; LONG CHAIN ACYL COENZYME A DEHYDROGENASE; PARVOVIRUS VECTOR;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CELL LEVEL; CONTROLLED STUDY; ELECTRON TRANSPORT; ELECTROSPRAY; ENZYME ACTIVITY; ENZYME DEFICIENCY; FATTY ACID OXIDATION; FATTY LIVER; FEMALE; GENE EXPRESSION; IMMUNOBLOTTING; IMMUNOHISTOCHEMISTRY; LIVER CELL; LONG CHAIN ACYL COENZYME A DEHYDROGENASE DEFICIENCY; MALE; MOUSE; NONHUMAN; NUCLEAR MAGNETIC RESONANCE SPECTROSCOPY; PORTAL VEIN; PRIORITY JOURNAL; TANDEM MASS SPECTROMETRY; TIBIALIS ANTERIOR MUSCLE; VIRAL GENE DELIVERY SYSTEM; VIRUS CAPSID; ADENO ASSOCIATED VIRUS; ANIMAL; GENE TRANSFER; GENE VECTOR; GENETIC TRANSDUCTION; GENETICS; LIVER; METABOLISM;

ADENO-ASSOCIATED VIRUS; MIRIDAE; MUS;

ACYL-COA DEHYDROGENASE, LONG-CHAIN; ANIMALS; DEPENDOVIRUS; FEMALE; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; LIVER; MALE; MICE; TRANSDUCTION, GENETIC;

EID: 58149188897     PISSN: 1099498X     EISSN: 15212254     Source Type: Journal    
DOI: 10.1002/jgm.1242     Document Type: Article

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