A combined artificial chromosome-stem cell therapy method in a model experiment aimed at the treatment of Krabbe's disease in the Twitcher mouse

Cellular and Molecular Life Sciences

Volumn 65, Issue 23, 2008, Pages 3830-3838

  Katona, R L ^a   Sinko I ^a   Hollo G ^a   Szucs, K Székely ^a   Praznovszky, T ^a   Kereso, J ^a   Csonka, E ^a   Fodor, K ^a   Cserpan I ^a   Szakal B ^a   Blazso P ^a   Udvardy, A ^a   Hadlaczky, G ^a  

^a INSTITUTE OF EXPERIMENTAL MEDICINE   (Hungary)

Author keywords

Gene therapy; Krabbe's disease; Mammalian artificial chromosome; Stem cell; Transgenic mouse

Indexed keywords

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CELL TYPE; CHROMOSOME; FEMALE; GENE TARGETING; GLOBOID CELL LEUKODYSTROPHY; KARYOTYPE; MONOGENIC DISORDER; MOUSE; NONHUMAN; STEM CELL TRANSPLANTATION;

ANIMALS; CHIMERA; CHROMOSOMES, ARTIFICIAL, MAMMALIAN; GENE THERAPY; GENETIC VECTORS; IN SITU HYBRIDIZATION, FLUORESCENCE; KARYOTYPING; LEUKODYSTROPHY, GLOBOID CELL; MICE; MICE, TRANSGENIC; PLURIPOTENT STEM CELLS; STEM CELL TRANSPLANTATION; TRANSFECTION; TRANSGENES;

MAMMALIA; MUS; MUS MUSCULUS;

EID: 57349120065     PISSN: 1420682X     EISSN: 15691632     Source Type: Journal    
DOI: 10.1007/s00018-008-8442-2     Document Type: Article

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