Idebenone treatment in paediatric and adult patients with Friedreich ataxia: Long-term follow-up

European Journal of Paediatric Neurology

Volumn 12, Issue 6, 2008, Pages 470-475

  Pineda, Mercè ^a   Arpa, Javier ^b   Montero, Raquel ^a   Aracil, Asunción ^a   Domínguez, Francisco ^b   Galván, Marta ^a   Mas, Anna ^a   Martorell, Loreto ^a   Sierra, Cristina ^a   Brandi, Nuria ^a   García Arumí, Elena ^c   Rissech, Miquel ^a   Velasco, Daniel ^a   Costa, Juan A ^b   Artuch, Rafael ^a  

^a HOSPITAL SANT JOAN DE DÉU   (Spain)

^b HOSPITAL UNIVERSITARIO LA PAZ   (Spain)

^c HOSPITAL UNIVERSITARI VALL D HEBRON   (Spain)

Author keywords

Cerebellar ataxia; Friedreich ataxia; Hypertrophic cardiomyopathy; ICARS; Idebenone treatment; Paediatric patients

Indexed keywords

CATALASE; GLUTATHIONE PEROXIDASE; GLUTATHIONE REDUCTASE; IDEBENONE; MALONALDEHYDE; RETINOL; SELENIUM; SUPEROXIDE DISMUTASE; TOCOPHEROL; UBIDECARENONE; ZINC;

ABSENCE OF SIDE EFFECTS; ADOLESCENT; ADULT; ANTIOXIDANT ACTIVITY; ARTICLE; BLOOD ANALYSIS; CARDIOMYOPATHY; CLINICAL ARTICLE; CLINICAL TRIAL; CONTROLLED STUDY; DOSE RESPONSE; DRUG BLOOD LEVEL; DRUG DOSE INCREASE; DRUG EFFECT; DRUG EFFICACY; ECHOCARDIOGRAPHY; FEMALE; FOLLOW UP; FRIEDREICH ATAXIA; GAIT DISORDER; GROUPS BY AGE; HEART EJECTION FRACTION; HEART LEFT VENTRICLE MASS; HEART VENTRICLE SEPTUM; HEART VENTRICLE WALL; HUMAN; MALE; NEUROLOGIC DISEASE; NEUROLOGIC EXAMINATION; OPEN STUDY; OPTIMAL DRUG DOSE; PRIORITY JOURNAL; PROSPECTIVE STUDY; RATING SCALE; SCHOOL CHILD; SPEECH DISORDER; TREATMENT DURATION; TREATMENT RESPONSE;

ADOLESCENT; ADULT; ANTIOXIDANTS; CHILD; ECHOCARDIOGRAPHY; FEMALE; FOLLOW-UP STUDIES; FRIEDREICH ATAXIA; HEART DISEASES; HEART FUNCTION TESTS; HUMANS; MALE; NEUROLOGIC EXAMINATION; NEUROPSYCHOLOGICAL TESTS; TREATMENT OUTCOME; UBIQUINONE; YOUNG ADULT;

EID: 52249089314     PISSN: 10903798     EISSN: 15322130     Source Type: Journal    
DOI: 10.1016/j.ejpn.2007.11.006     Document Type: Article

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