Phenotypic correction of ornithine transcarbamylase deficiency using low dose helper-dependent adenoviral vectors

Journal of Gene Medicine

Volumn 10, Issue 8, 2008, Pages 890-896

  Brunetti Pierri, Nicola ^a   Clarke, Christian ^a   Mane, Viraj ^a   Palmer, Donna J ^a   Lanpher, Brendan ^a   Sun, Qin ^a   O'Brien, William ^a   Lee, Brendan ^a  

^a BAYLOR COLLEGE OF MEDICINE   (United States)

Author keywords

Gene therapy; Helper dependent adenoviral vectors; Liver directed gene therapy; Ornithine transcarbamylase deficiency; Urea cycle disorders

Indexed keywords

ADENOVIRUS VECTOR; HELPER DEPENDENT ADENOVIRUS VECTOR; ORNITHINE CARBAMOYLTRANSFERASE; OROTIC ACID;

ANIMAL EXPERIMENT; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; DISORDERS OF AMINO ACID AND PROTEIN METABOLISM; GENE EXPRESSION; HELPER VIRUS; HISTOCHEMISTRY; HYDRODYNAMICS BASED TRANSFECTION; LOW DRUG DOSE; MALE; MOUSE; NONHUMAN; PHENOTYPE; PRIORITY JOURNAL; TRANSGENE; VIRAL GENE DELIVERY SYSTEM; VIRAL GENE THERAPY;

ADENOVIRIDAE; AMINO ACID METABOLISM, INBORN ERRORS; ANIMALS; DISEASE MODELS, ANIMAL; GENE THERAPY; GENETIC VECTORS; HELPER VIRUSES; HISTOCYTOCHEMISTRY; LIVER; MICE; MICE, MUTANT STRAINS; ORNITHINE CARBAMOYLTRANSFERASE; OROTIC ACID; TRANSGENES;

MUS;

EID: 49349092841     PISSN: 1099498X     EISSN: 15212254     Source Type: Journal    
DOI: 10.1002/jgm.1218     Document Type: Article

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