Nuclear-targeted chimeric vector enhancing nonviral gene transfer into skeletal muscle of Fabry mice in vivo

FASEB Journal

Volumn 22, Issue 6, 2008, Pages 2097-2107

  Lavigne, Matthieu D ^a,b   Yates, Laura ^a   Coxhead, Peter ^a   Górecki, Dariusz C ^a,c  

^a UNIVERSITY OF PORTSMOUTH   (United Kingdom)

^b BIOMEDICAL RESEARCH FOUNDATION   (Greece)

^c Institute of Biomedical and Biomolecular Sciences   (United Kingdom)

Author keywords

Cell penetration peptides; Gene therapy; Pluronic; TAT

Indexed keywords

ALPHA GALACTOSIDASE; CYCLOPHOSPHAMIDE; DNA BINDING PROTEIN; TRANSACTIVATOR PROTEIN;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; ATOMIC FORCE MICROSCOPY; BINDING SITE; CHIMERA; COMPLEX FORMATION; CONTROLLED STUDY; FABRY DISEASE; GEL MOBILITY SHIFT ASSAY; GENE EXPRESSION; IN VITRO STUDY; MOLECULAR INTERACTION; MOUSE; NONHUMAN; NONVIRAL GENE DELIVERY SYSTEM; PRIORITY JOURNAL; SKELETAL MUSCLE; STOICHIOMETRY; TRANSCRIPTION INITIATION;

ALPHA-GALACTOSIDASE; ANIMALS; CELL NUCLEUS; DEOXYRIBONUCLEASES, TYPE I SITE-SPECIFIC; DISEASE MODELS, ANIMAL; FABRY DISEASE; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; MICE; MUSCLE, SKELETAL;

MUS;

EID: 44949092569     PISSN: 08926638     EISSN: None     Source Type: Journal    
DOI: 10.1096/fj.07-093765     Document Type: Article

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