The role of cis-regulatory elements in the design of gene therapy vectors for inherited blindness

Expert Opinion on Biological Therapy

Volumn 8, Issue 5, 2008, Pages 599-608

  Corbo, Joseph C ^a  

^a WASHINGTON UNIVERSITY SCHOOL OF MEDICINE   (United States)

Author keywords

Adeno associated virus; Blindness; cis regulatory elements; Gene therapy; Photoreceptors; Retina

Indexed keywords

ADENOVIRUS VECTOR; CIS ACTING ELEMENT; CIS REGULATORY ELEMENT; LENTIVIRUS VECTOR; PARVOVIRUS VECTOR; VIRUS VECTOR;

BLINDNESS; CELL TYPE; DRUG DESIGN; GENE EXPRESSION REGULATION; GENE LOCUS; GENE OVEREXPRESSION; GENE TARGETING; NONHUMAN; PHOTORECEPTOR; PIGMENT EPITHELIUM; RETINA CONE; RETINA DISEASE; RETINA GANGLION CELL; RETINA ROD; REVIEW; RNA INTERFERENCE; TRANSCRIPTION REGULATION; TRANSGENE; VIRAL GENE DELIVERY SYSTEM; VIRAL GENE THERAPY;

ANIMALS; BLINDNESS; DEPENDOVIRUS; GENE THERAPY; GENETIC VECTORS; HUMANS; REGULATORY SEQUENCES, NUCLEIC ACID;

ADENO-ASSOCIATED VIRUS; ANIMALIA;

EID: 43649085073     PISSN: 14712598     EISSN: None     Source Type: Journal    
DOI: 10.1517/14712598.8.5.599     Document Type: Review

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