Transduction of full-length dystrophin to multiple skeletal muscles improves motor performance and life span in utrophin/dystrophin double knockout mice

Molecular Therapy

Volumn 16, Issue 5, 2008, Pages 825-831

  Kawano, Ryoko ^a   Ishizaki, Masatoshi ^a   Maeda, Yasushi ^a   Uchida, Yuji ^b   Kimura, En ^a   Uchino, Makoto ^a  

^a KUMAMOTO UNIVERSITY   (Japan)

^b SOJO UNIVERSITY   (Japan)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; ALPHA SARCOGLYCAN; BETA DYSTROGLYCAN; COMPLEMENTARY DNA; DYSTROPHIN; MYC PROTEIN; NEURONAL NITRIC OXIDE SYNTHASE; UTROPHIN;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; CONVALESCENCE; DUCHENNE MUSCULAR DYSTROPHY; EMBRYO; GENE EXPRESSION; GENETIC TRANSDUCTION; HUMAN; HUMAN CELL; KNOCKOUT MOUSE; LIFESPAN; MOTOR PERFORMANCE; MOUSE; MUSCLE CELL; MUSCLE FUNCTION; NONHUMAN; SKELETAL MUSCLE; TREATMENT OUTCOME; VIRAL GENE DELIVERY SYSTEM; WEIGHT GAIN;

ADENOVIRIDAE; MURINAE; MUS;

EID: 42549160852     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2008.23     Document Type: Article

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