Do orphan medicines benefit patients?

Pharmaceutical Journal

Volumn 280, Issue 7490, 2008, Pages 216-218

  Holding, Jackie ^a  

^a NONE

Author keywords

[No Author keywords available]

Indexed keywords

BETAINE; CELECOXIB; CLOFARABINE; DASATINIB; DEFERASIROX; ECULIZUMAB; GALSULFASE; HYDROXYUREA; IDURONATE 2 SULFATASE; LENALIDOMIDE; NELARABINE; ORPHAN DRUG; RAZOXANE; RECOMBINANT SOMATOMEDIN C; RUFINAMIDE; SIKLOS; SITAXSENTAN; SORAFENIB; STIRIPENTOL; SUNITINIB;

ACUTE LYMPHOBLASTIC LEUKEMIA; ADENOMATOUS POLYP; ANTISENSE THERAPY; ARTICLE; AUSTRALIA; CELL THERAPY; CHRONIC MYELOID LEUKEMIA; EUROPE; EXTRAVASATION; FINANCIAL MANAGEMENT; FOOD AND DRUG ADMINISTRATION; GASTROINTESTINAL STROMAL TUMOR; GENE THERAPY; GOVERNMENT; HEALTH CARE ACCESS; HEALTH CARE ORGANIZATION; HOMOCYSTINURIA; HORMONE DEFICIENCY; HUMAN; HUNTER SYNDROME; IRON OVERLOAD; JAPAN; KIDNEY CARCINOMA; LAW; LENNOX GASTAUT SYNDROME; MAROTEAUX LAMY SYNDROME; MULTIPLE MYELOMA; MYOCLONUS EPILEPSY; PAROXYSMAL NOCTURNAL HEMOGLOBINURIA; PATIENT CARE; PHARMACEUTICAL CARE; PREVALENCE; PULMONARY HYPERTENSION; SICKLE CELL ANEMIA; SINGAPORE; THROMBOEMBOLISM; UNITED KINGDOM; UNITED STATES;

EID: 40449112644     PISSN: 00316873     EISSN: None     Source Type: Journal    
DOI: None     Document Type: Article

References (3)

1. de Varax, Lettellier M. Bortlein G. Alcimed study on orphan drugs. Available at http://ec.europa.eu (accessed on 11 February 2008).
2. Drummond MF, Wilson D, Kanavos P, Ubel P, Rovira J. Assesssing the economic challenges posed by orphan drugs. International Journal of Technology Assessment in Health Care 2007;23:36-42.
3. European Commission. Inventory of community and member states' incentive measures to aid the research, marketing, development and availability of orphan medicinal products. Available at http://ec.europa.eu (accessed on 11 February 2008).