Is sapropterin treatment suitable for all subjects with phenylketonuria?

Expert Opinion on Pharmacotherapy

Volumn 9, Issue 1, 2008, Pages 145-147

  Doggrell, Sheila A ^a  

^a RMIT UNIVERSITY   (Australia)

Author keywords

Clinical trials; Phenylalanine; Phenylketonuria; Sapropterin

Indexed keywords

PHENYLALANINE; PLACEBO; SAPROPTERIN;

ADOLESCENT; ADULT; AMINO ACID BLOOD LEVEL; ARTICLE; BLOOD ANALYSIS; CLINICAL TRIAL; CONTROLLED CLINICAL TRIAL; CONTROLLED STUDY; DIETARY INTAKE; DRUG EFFICACY; DRUG RESPONSE; DRUG SAFETY; DRUG TOLERABILITY; FEMALE; FOLLOW UP; HUMAN; MALE; OUTCOME ASSESSMENT; PHASE 3 CLINICAL TRIAL; PHENYLKETONURIA; PROTEIN RESTRICTION; RANDOMIZED CONTROLLED TRIAL; REFERENCE VALUE; REPEATED DRUG DOSE; SCHOOL CHILD; TREATMENT DURATION; UNSPECIFIED SIDE EFFECT;

ADOLESCENT; ADULT; BIOPTERIN; CLINICAL TRIALS, PHASE III AS TOPIC; EXPERT TESTIMONY; FEMALE; HUMANS; MALE; PHENYLALANINE; PHENYLKETONURIAS; TREATMENT OUTCOME;

EID: 39049136890     PISSN: 14656566     EISSN: None     Source Type: Journal    
DOI: 10.1517/14656566.9.1.145     Document Type: Article

References (7)

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