Correction of enzyme levels with allogeneic hematopoeitic progenitor cell transplantation in Niemann-Pick type B

Pediatric Blood and Cancer

Volumn 49, Issue 7, 2007, Pages 987-989

  Schneiderman, Jennifer ^a,b   Thormann, Kimberly ^a   Charrow, Joel ^a   Kletzel, Morris ^a  

^a CHILDREN'S MEMORIAL HOSPITAL   (United States)

^b Box #30 ^*  (United States)

Author keywords

Metabolic disorders; Niemann Pick; Therapy; Transplantation

Indexed keywords

CITRATE DISODIUM; CYCLOPHOSPHAMIDE; CYCLOSPORIN; METHOTREXATE; PREDNISONE; SPHINGOMYELIN PHOSPHODIESTERASE; THIOTEPA;

ALLOGENEIC HEMATOPOIETIC STEM CELL TRANSPLANTATION; ARTICLE; BONE MARROW BIOPSY; CASE REPORT; CLINICAL FEATURE; ENZYME BLOOD LEVEL; FEMALE; GRAFT VERSUS HOST REACTION; HLA MATCHING; HUMAN; IMMUNOSUPPRESSIVE TREATMENT; INFANT; KIDNEY TUBULE ACIDOSIS; LEUKOCYTE; NIEMANN PICK DISEASE; OUTCOME ASSESSMENT; PRIORITY JOURNAL; SKIN FIBROBLAST; SPLENOMEGALY; SYMPTOM; THROMBOCYTOPENIA; TREATMENT FAILURE; WHOLE BODY RADIATION;

BONE MARROW TRANSPLANTATION; CELLS, CULTURED; FEMALE; FIBROBLASTS; GRAFT VS HOST DISEASE; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMANS; INFANT; LEUKOCYTES, MONONUCLEAR; NIEMANN-PICK DISEASE, TYPE B; SIBLINGS; SPHINGOMYELIN PHOSPHODIESTERASE; TRANSPLANTATION CONDITIONING; TRANSPLANTATION, HOMOLOGOUS; TREATMENT OUTCOME;

EID: 35648941563     PISSN: 15455009     EISSN: 15455017     Source Type: Journal    
DOI: 10.1002/pbc.21300     Document Type: Article

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