A first therapy for Niemann-Pick C

Lancet Neurology

Volumn 6, Issue 9, 2007, Pages 748-749

  Erickson, Robert P ^a  

^a UNIVERSITY OF ARIZONA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

CERAMIDE GLUCOSYLTRANSFERASE; CHOLESTEROL; CYCLODEXTRIN DERIVATIVE; GANGLIOSIDE; GANGLIOSIDE GM2; GLYCOLIPID; LOW DENSITY LIPOPROTEIN RECEPTOR; MIGLUSTAT; NIFEDIPINE; RAB PROTEIN;

BRAIN CORTEX; CAT; CHOLESTEROL TRANSPORT; ENDOPLASMIC RETICULUM; GENE MUTATION; GOLGI COMPLEX; HIPPOCAMPUS; LETTER; MOUSE STRAIN; NEUROPATHOLOGY; NIEMANN PICK DISEASE; NONHUMAN; PRIORITY JOURNAL; SACCADIC EYE MOVEMENT;

CARRIER PROTEINS; CHOLESTEROL; ENZYME INHIBITORS; HUMANS; MEMBRANE GLYCOPROTEINS; MODELS, BIOLOGICAL; NIEMANN-PICK DISEASE, TYPE C;

EID: 34547785058     PISSN: 14744422     EISSN: None     Source Type: Journal    
DOI: 10.1016/S1474-4422(07)70198-9     Document Type: Letter

References (11)

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