Metabolic correction induced by leptin replacement treatment in young children with Berardinelli-Seip congenital lipoatrophy

Pediatrics

Volumn 120, Issue 2, 2007, Pages

  Beltrand, Jacques ^a,b   Beregszaszi, Marta ^a,b   Chevenne, Didier ^b   Sebag, Guy ^b   De Kerdanet, Marc ^b   Huet, Frédéric ^c   Polak, Michel ^d   Tubiana Rufi, Nadia ^e   Lacombe, Didier ^f   De Paoli, Alex M ^g   Levy Marchal, Claire ^a  

^a UNIVERSITÉ PARIS DESCARTES   (France)

^b HÔPITAL ROBERT DEBRÉ   (France)

^c South Hospital   (France)

^d Children Hospital   (France)

^e HÔPITAL NECKER ENFANTS MALADES   (France)

^f HÔPITAL PELLEGRIN   (France)

^g AMGEN INC   (United States)

Author keywords

Berardinelli Seip syndrome; Congenital lipoatrophy; Leptin

Indexed keywords

INSULIN; RECOMBINANT LEPTIN; RECOMBINANT METHIONYLLEPTIN; TRIACYLGLYCEROL; UNCLASSIFIED DRUG;

ADOLESCENT; ARTICLE; BERARDINELLI SEIP SYNDROME; CHILD; CLINICAL ARTICLE; CLINICAL TRIAL; DRUG EFFICACY; DRUG SAFETY; FATTY LIVER; FEMALE; HUMAN; HYPERTRIGLYCERIDEMIA; INJECTION SITE REACTION; INSULIN BLOOD LEVEL; INSULIN RESISTANCE; INSULIN SENSITIVITY; LIPOATROPHY; MALE; METABOLIC DISORDER; PRIORITY JOURNAL; RARE DISEASE; TREATMENT DURATION; TREATMENT OUTCOME; TRIACYLGLYCEROL BLOOD LEVEL;

ADOLESCENT; CHILD; CHILD, PRESCHOOL; FEMALE; HUMANS; LEPTIN; LIPODYSTROPHY, CONGENITAL GENERALIZED; MALE; PROSPECTIVE STUDIES;

EID: 34547652977     PISSN: 00314005     EISSN: 02105721     Source Type: Journal    
DOI: 10.1542/peds.2006-3165     Document Type: Article

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