Ex vivo gene therapy cures a blistering skin disease

Trends in Molecular Medicine

Volumn 13, Issue 6, 2007, Pages 219-222

  Featherstone, Carol ^a   Uitto, Jouni ^b  

^a Jefferson Institute of Molecular Medicine ^*  (France)

^b THOMAS JEFFERSON UNIVERSITY   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

KALININ; LAMININ 5 BETA3; RETROVIRUS VECTOR; UNCLASSIFIED DRUG;

BLISTER; CLINICAL TRIAL; EPIDERMOLYSIS BULLOSA; EPITHELIUM CELL; EX VIVO GENE TRANSFER; GENE THERAPY; GENETIC TRANSDUCTION; HUMAN; INHERITANCE; SHORT SURVEY; STEM CELL TRANSPLANTATION; TISSUE ENGINEERING; TREATMENT INDICATION;

CLINICAL TRIALS AS TOPIC; EPIDERMOLYSIS BULLOSA; GENE THERAPY; HUMANS; ORPHAN DRUG PRODUCTION; STEM CELL TRANSPLANTATION; STEM CELLS;

EID: 34249712431     PISSN: 14714914     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.molmed.2007.03.006     Document Type: Short Survey

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