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Volumn 13, Issue 6, 2006, Pages 525-531

RNAi: A potential therapy for the dominantly inherited nucleotide repeat diseases

Author keywords

Adeno associated virus vectors; Huntington's disease; Polyglutamine; RNAi; Spinocerebellar ataxia

Indexed keywords

ATAXIN 1; ATAXIN 3; ATAXIN 7; HUNTINGTIN; MYOTONIC DYSTROPHY PROTEIN KINASE; POLYGLUTAMINE; SHORT HAIRPIN RNA; SMALL INTERFERING RNA; ZINC FINGER PROTEIN;

EID: 33645135860     PISSN: 09697128     EISSN: 14765462     Source Type: Journal    
DOI: 10.1038/sj.gt.3302664     Document Type: Review
Times cited : (29)

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