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IBMTR/ABMTR Newsletter 1 February 2002. In this analysis of IBMTR data of 94 FA patients who underwent transplantation with alternative donor HCT, malformations (≥3), use of androgens before HCT, positive recipient cytomegalovirus serology, and use of female donor were associated with poor survival.
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0038621756
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Low-intensity hematopoietic stem-cell transplantation across human leucocyte antigen barriers in dyskeratosis congenita
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Dror Y, Freedman MH, Leaker M, et al. Low-intensity hematopoietic stem-cell transplantation across human leucocyte antigen barriers in dyskeratosis congenita. Bone Marrow Transplant 2003; 31:847-850. This paper reports successful unrelated donor BMT after FLU-based preparative therapy for dyskeratosis congenita.
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(2003)
Bone Marrow Transplant
, vol.31
, pp. 847-850
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Dror, Y.1
Freedman, M.H.2
Leaker, M.3
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50
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0037356063
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Nonmyeloablative allogeneic hematopoietic stem cell transplantation for treatment of dyskeratosis congenita
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Gungor T, Corbacioglu S, Storb R, et al. Nonmyeloablative allogeneic hematopoietic stem cell transplantation for treatment of dyskeratosis congenita. Bone Marrow Transplant 2003; 31:407-410. This case report describes successful HLA-identical sibling peripheral blood progenitor cell HCT after nonmyeloablative preparative therapy for patient with dyskeratosis congenita.
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(2003)
Bone Marrow Transplant
, vol.31
, pp. 407-410
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Gungor, T.1
Corbacioglu, S.2
Storb, R.3
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51
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1942538288
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Allogeneic stem cell transplantation for patients with congenital amegakaryocytic thrombocytopenia (CAT)
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Al-Ahmari A, Ayas M, Al-Jefri A, et al. Allogeneic stem cell transplantation for patients with congenital amegakaryocytic thrombocytopenia (CAT). Bone Marrow Transplant 2004; 33:829-831. This report describes busulfan-based preparative therapy for patients with amegakaryocytic thrombocytopenia undergoing HCT.
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(2004)
Bone Marrow Transplant
, vol.33
, pp. 829-831
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Al-Ahmari, A.1
Ayas, M.2
Al-Jefri, A.3
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