Paediatric non-neuronopathic Gaucher disease: Recommendations for treatment and monitoring

European Journal of Pediatrics

Volumn 163, Issue 2, 2004, Pages 67-75

  Baldellou, Antonio ^a   Andria, Generoso ^b   Campbell, Pauline E ^c   Charrow, Joel ^d   Cohen, Ian J ^e   Grabowski, Gregory A ^f   Harris, Chris M ^c   Kaplan, Paige ^g   McHugh, Kieran ^c   Mengel, Eugen ^h   Vellodi, Ashok ^a,c  

^a HOSPITAL UNIVERSITARIO MIGUEL SERVET   (Spain)

^b UNIVERSITY OF NAPLES FEDERICO II   (Italy)

^c GREAT ORMOND STREET HOSPITAL   (United Kingdom)

^d NORTHWESTERN UNIVERSITY   (United States)

^e TEL AVIV UNIVERSITY   (Israel)

^f CINCINNATI CHILDREN S HOSPITAL RESEARCH FOUNDATION   (United States)

^g UNIVERSITY OF PENNSYLVANIA   (United States)

^h JOHANNES GUTENBERG UNIVERSITY   (Germany)

Author keywords

Gaucher disease; Management; Monitoring; Paediatric; Quality of life

Indexed keywords

CHITOTRIOSIDASE; ENZYME; GLUCOSYLCERAMIDE; HEMOGLOBIN; UNCLASSIFIED DRUG;

ARTICLE; CONTROLLED STUDY; DISEASE ASSOCIATION; DISEASE COURSE; DISEASE SEVERITY; ENZYME BLOOD LEVEL; ENZYME THERAPY; GAUCHER DISEASE; HUMAN; MEDICAL ASSESSMENT; MEDICAL EXAMINATION; MORBIDITY; PATIENT MONITORING; PEDIATRICS; PHENOTYPE; PHYSICAL EXAMINATION; PRIORITY JOURNAL; QUALITY OF LIFE; RISK FACTOR; THROMBOCYTE COUNT;

BONE DENSITY; CHILD, PRESCHOOL; ENZYMES; GAUCHER DISEASE; HUMANS; QUALITY OF LIFE;

EID: 10744229163     PISSN: 03406199     EISSN: None     Source Type: Journal    
DOI: 10.1007/s00431-003-1363-z     Document Type: Article

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