Unsuccessful chimeraplast strategy for the correction of a mutation causing Gaucher disease

Blood Cells, Molecules, and Diseases

Volumn 31, Issue 2, 2003, Pages 183-186

  Diaz Font, Anna ^a   Cormand, Bru ^a   Chabás, Amparo ^b   Vilageliu, Lluïsa ^a   Grinberg, Daniel ^a  

^a UNIVERSITY OF BARCELONA   (Spain)

^b HOSPITAL CLÍNIC   (Spain)

Author keywords

C.1448C >T (L444P) mutation; Chimeraplasts; Gaucher disease; Gene therapy

Indexed keywords

ARTICLE; BACTERIAL CELL; CELL FREE SYSTEM; CHIMERAPLASTY; ESCHERICHIA COLI; FIBROBLAST; GAUCHER DISEASE; GENE MUTATION; HUMAN; IN VITRO STUDY; MISMATCH REPAIR; NONHUMAN; PRIORITY JOURNAL; CONTROLLED STUDY; DNA REPAIR; EVALUATION; GENE LOCATION; GENE REPLICATION; GENOME; HOMOZYGOSITY; HUMAN CELL; LIVER CELL; POPULATION GENETICS; PREVALENCE;

ESCHERICHIA COLI;

RETROVIRUS VECTOR;

EID: 0347383863     PISSN: 10799796     EISSN: None     Source Type: Journal    
DOI: 10.1016/S1079-9796(03)00157-8     Document Type: Article

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